ACCELERATE: A Patient-Powered Natural History Study Design Enabling Clinical and Therapeutic Discoveries in a Rare Disorder by Pierson, Sheila K., Khor, Johnson S., Ziglar, Jasira, Liu, Amy, Floess, Katherine, NaPier, Erin, Gorzewski, Alexander M., Tamakloe, Mark-Avery, Powers, Victoria, Akhter, Faizaan, Haljasmaa, Eric, Jayanthan, Raj, Rubenstein, Arthur, Repasky, Mileva, Elenitoba-Johnson, Kojo, Ruth, Jason, Jacobs, Bette, Streetly, Matthew, Angenendt, Linus, Patier, Jose Luis, Ferrero, Simone, Zinzani, Pier Luigi, Terriou, Louis, Casper, Corey, Jaffe, Elaine, Hoffmann, Christian, Oksenhendler, Eric, Fosså, Alexander, Srkalovic, Gordan, Chadburn, Amy, Uldrick, Thomas S., Lim, Megan, van Rhee, Frits, Fajgenbaum, David C.

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Natural History Study of Idiopathic Multicentric Castleman Disease Identifies Effective Treatments for a Large Proportion of Patients but Treatment-Refractory Patients Remain by Pierson, Sheila K, Ren, Yue, Khor, Johnson, Haljasmaa, Eric, Ziglar, Jasira, Floess, Katherine, NaPier, Erin, Akhter, Faizaan, Liu, Amy Y, Gibson, Damilola, Kanhai, Karan, Martin, Rabecka, Chadburn, Amy, Srkalovic, Gordan, Lim, Megan S., Casper, Corey, Uldrick, Thomas S., Jaffe, Elaine S., van Rhee, Frits, Lee, Hongzhe, Fajgenbaum, David C

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