Development of an in vitro genotoxicity assay to detect retroviral vector-induced lymphoid insertional mutants by Bastone, Antonella L., Dziadek, Violetta, John-Neek, Philipp, Mansel, Friederike, Fleischauer, Jenni, Agyeman-Duah, Eric, Schaudien, Dirk, Dittrich-Breiholz, Oliver, Schwarzer, Adrian, Schambach, Axel, Rothe, Michael

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Predicting genotoxicity of viral vectors for stem cell gene therapy using gene expression-based machine learning by Schwarzer, Adrian, Talbot, Steven R., Selich, Anton, Morgan, Michael, Schott, Juliane W., Dittrich-Breiholz, Oliver, Bastone, Antonella L., Weigel, Bettina, Ha, Teng Cheong, Dziadek, Violetta, Gijsbers, Rik, Thrasher, Adrian J., Staal, Frank J.T., Gaspar, Hubert B., Modlich, Ute, Schambach, Axel, Rothe, Michael

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Haematopoietic gene therapy of non-conditioned patients with Fanconi anaemia-A: results from open-label phase 1/2 (FANCOLEN-1) and long-term clinical trials by Río, Paula, Zubicaray, Josune, Navarro, Susana, Gálvez, Eva, Sánchez-Domínguez, Rebeca, Nicoletti, Eileen, Sebastián, Elena, Rothe, Michael, Pujol, Roser, Bogliolo, Massimo, John-Neek, Philipp, Bastone, Antonella Lucía, Schambach, Axel, Wang, Wei, Schmidt, Manfred, Larcher, Lise, Segovia, José C, Yáñez, Rosa M, Alberquilla, Omaira, Díez, Begoña, Fernández-García, María, García-García, Laura, Ramírez, Manuel, Galy, Anne, Lefrere, Francois, Cavazzana, Marina, Leblanc, Thierry, García de Andoin, Nagore, López-Almaraz, Ricardo, Catalá, Albert, Barquinero, Jordi, Rodríguez-Perales, Sandra, Rao, Gayatri, Surrallés, Jordi, Soulier, Jean, Díaz-de-Heredia, Cristina, Schwartz, Jonathan D, Sevilla, Julián, Bueren, Juan A, Río, Paula, Zubicaray, Josune, Navarro, Susana, Gálvez, Eva, Sánchez-Domínguez, Rebeca, Nicoletti, Eileen, Sebastián, Elena, Rothe, Michael, Pujol, Roser, Bogliolo, Massimo, John-Neek, Philipp, Bastone, Antonella L, Schambach, Axel, Wang, Wei, Schmidt, Manfred, Larcher, Lise, Segovia, José C, Yáñez, Rosa M, Pérez-Maroto, Florencio, de la Cruz, Ana, Casado, José A, Giménez, Yari, Álvarez, Lara, Alberquilla, Omaira, Díez, Begoña, Fernández-García, María, García-García, Laura, Gómez, Ana, Galán, Almudena, Ramírez, Manuel, Salgado, Rocío, Galy, Anne, Lefrere, Francois, Cavazzana, Marina, Leblanc, Thierry, Garcia de Andoin, Nagore, López-Almaraz, Ricardo, Catalá, Albert, Barquinero, Jordi, Rodríguez-Perales, Sandra, Rao, Gayatri, Surrallés, Jordi, Soulier, Jean, Díaz-de-Heredia, Cristina, Schwartz, Jonathan D, Sevilla, Julián, Bueren, Juan A

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Lentiviral-Mediated Gene Therapy for Patients with Fanconi Anemia [Group a]: Updated Results from Global RP-L102 Clinical Trials by Czechowicz, Agnieszka D., Sevilla, Julián, Booth, Claire, Zubicaray, Josune, Rio, Paula, Navarro, Susana, Cherry, Kritika, O'Toole, Gráinne, Xu-Bayford, Jinhua, Ancliff, Philip, Sebastián, Elena, Rothe, Michael, Bastone, Antonella L, John-Neek, Philipp, Schambach, Axel, Wang, Wei, Choi, Grace, Zeini, Miriam, Nicoletti, Eileen, Eide, Cindy, Wagner, John E, Rao, Gayatri R, Thrasher, Adrian J., Roncarolo, Maria-Grazia, Schwartz, Jonathan D, Bueren, Juan A, Agarwal, Rajni

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