O.9 First-in-human phase I study to assess safety, tolerability and dose for intrathecal injection of ISIS-SMNRx in SMA patients by Swoboda, K, Chiriboga, C, Darras, B, Iannaccone, S, Montes, J, Rausch, N, Parad, R, Johnson, S, Vivo, D. De, Norris, D, Alexander, K, Bennet, F.C, Bishop, K

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