Improving Gene Editing Outcomes in Human Hematopoietic Stem and Progenitor Cells by Temporal Control of DNA Repair by Lomova, Anastasia, Clark, Danielle N., Campo‐Fernandez, Beatriz, Flores‐Bjurström, Carmen, Kaufman, Michael L., Fitz‐Gibbon, Sorel, Wang, Xiaoyan, Miyahira, Eric Y., Brown, Devin, DeWitt, Mark A., Corn, Jacob E., Hollis, Roger P., Romero, Zulema, Kohn, Donald B.

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Regulation and Function of Lentiviral Vector-Mediated TCIRG1 Expression in Osteoclasts from Patients with Infantile Malignant Osteopetrosis: Implications for Gene Therapy by Thudium, Christian Schneider, Moscatelli, Ilana, Löfvall, Henrik, Kertész, Zsuzsanna, Montano, Carmen, Bjurström, Carmen Flores, Karsdal, Morten Asser, Schulz, Ansgar, Richter, Johan, Henriksen, Kim

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Lentiviral gene transfer of TCIRG1 into peripheral blood CD34+ cells restores osteoclast function in infantile malignant osteopetrosis by Moscatelli, Ilana, Thudium, Christian Schneider, Flores, Carmen, Schulz, Ansgar, Askmyr, Maria, Gudmann, Natasja Stæhr, Andersen, Nanna Merete, Porras, Oscar, Karsdal, Morten Asser, Villa, Anna, Fasth, Anders, Henriksen, Kim, Richter, Johan

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A Comparison of Osteoclast-Rich and Osteoclast-Poor Osteopetrosis in Adult Mice Sheds Light on the Role of the Osteoclast in Coupling Bone Resorption and Bone Formation by Thudium, Christian S., Moscatelli, Ilana, Flores, Carmen, Thomsen, Jesper S., Brüel, Annemarie, Gudmann, Natasja Stæhr, Hauge, Ellen-Margrethe, Karsdal, Morten A., Richter, Johan, Henriksen, Kim

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Preservation of Gene Edited Hematopoietic Stem Cells By Transient Overexpression of BCL-2 mRNA by Bjurström, Carmen Flores, Mojadidi, Michelle, Lomova, Anastasia, Lai, Stephen, Fitz-Gibbon, Sorel, Pellegrini, Matteo, Cooper, Aaron R, Lill, Georgia R, Kaufman, Michael, Cost, Gregory J, Holmes, Michael C., Hollis, Roger P, Kohn, Donald B

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Dissociation of bone resorption and bone formation in adult mice with a non-functional V-ATPase in osteoclasts leads to increased bone strength by Henriksen, Kim, Flores, Carmen, Thomsen, Jesper S, Brüel, Anne-Marie, Thudium, Christian S, Neutzsky-Wulff, Anita V, Langenbach, Geerling E J, Sims, Natalie, Askmyr, Maria, Martin, Thomas J, Everts, Vincent, Karsdal, Morten A, Richter, Johan

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Osteoclasts are not crucial for hematopoietic stem cell maintenance in adult mice by Flores, Carmen, Moscatelli, Ilana, Thudium, Christian S, Gudmann, Natasja Stæhr, Thomsen, Jesper S, Brüel, Annemarie, Karsdal, Morten A, Henriksen, Kim, Richter, Johan

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Nonablative neonatal bone marrow transplantation rapidly reverses severe murine osteopetrosis despite low‐level engraftment and lack of selective expansion of the osteoclastic line... by Flores, Carmen, de Vries, Teun J, Moscatelli, Ilana, Askmyr, Maria, Schoenmaker, Ton, Langenbach, Geerling EJ, Ehinger, Mats, Everts, Vincent, Richter, Johan

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Low-dose busulphan conditioning and neonatal stem cell transplantation preserves vision and restores hematopoiesis in severe murine osteopetrosis by Askmyr, Maria, Holmberg, Johan, Flores, Carmen, Ehinger, Mats, Hjalt, Tord, Richter, Johan

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Dissociation of bone resorption and bone formation in adult mice transplanted with OC/OC hematopoietic stem cells by Henriksen, K, Flores, C, Neutzsky-Wulff, A.V, Jensen, V.K, Richter, J, Karsdal, M.A

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Neonatal bone marrow transplantation without prior conditioning rapidly reverses osteopetrosis in oc/oc mice despite only minimal donor cell engraftment by Flores, C, de Vries, T.J, Askmyr, M.K, Schoenmaker, T, Ehinger, M, Everts, V, Richter, J

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