Case report: Novel treatment regimen for enterovirus encephalitis in SCID by Chetty, Kritika, Cheng, Iek, Kaliakatsos, Marios, Gonzalez-Granado, Luis Ignacio, Klapsa, Dimitra, Martin, Javier, Bamford, Alasdair, Breuer, Judith, Booth, Claire

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Severe Leukocyte Adhesion Deficiency-I (LAD-I) Lentiviral-Mediated Ex-Vivo Gene Therapy: Ongoing Phase 1/2 Study Results by Booth, Claire, Sevilla, Julian, Lopez, Maria Chitty, Almarza, Elena, Zubicaray, Josune, Chetty, Kritika, Moore, Theodore, Bueren, Juan, Schwartz, Jonathan, Kohn, Donald

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Lentiviral-mediated Gene Therapy for Patients with Fanconi Anemia [Group A]: Updated Results from Global RP-L102 Clinical Trials by Czechowicz, Agnieszka, Sevilla, Julián, Booth, Claire, Agarwal, Rajni, Zubicaray, Josune, Río, Paula, Navarro, Susana, Chetty, Kritika, O'Toole, Grainne, Xu-Bayford, Jinhua, Ancliff, Philip, Sebastián, Elena, Choi, Grace, Zeini, Miriam, Nicoletti, Eileen, Wagner, John E, Rao, Gayatri R., Thrasher, Adrian J., Schwartz, Jonathan D., Roncarolo, Maria Grazia, Bueren, Juan A.

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Lentiviral Gene Therapy with Low Dose Conditioning for X-Linked SCID Results in Complete Immune Reconstitution and No Evidence of Clonal Expansion by Booth, Claire, Kohn, Donald B., Armant, Myriam, Prockop, Susan, Buckland, Karen, Chandra, Sharat, Chandrakasan, Shanmuganathan, Chetty, Kritika, Dansereau, Colleen, de Oliveira, Satiro, Everett, John, León Rico, Diego, London, Wendy B., Xu-Bayford, Jin Hua, Moore, Theodore B., Nagarsheth, Nisha, Parikh, Suhag, Terrazas, Dayna, White, Shanna L, Schambach, Axel, Bushman, Frederic D., Thrasher, Adrian J., Williams, David A., Pai, Sung-Yun

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Interim Results from an Ongoing Phase 1/2 Study of Lentiviral-mediated Ex-vivo Gene Therapy for Pediatric Patients with Severe Leukocyte Adhesion Deficiency-I (LAD-I) by Booth, Claire, Sevilla, Julián, Rao, Gayatri R., Chitty Lopez, Maria, Almarza, Elena, Terrazas, Dayna, Zubicaray, Josune, González Vicent, Marta, Chetty, Kritika, O'Toole, Grainne, Xu-Bayford, Jinhua, Nicoletti, Eileen, Fernandes, Augustine, Kuo, Caroline, de Oliveira, Satiro, Moore, Theodore B., Choi, Grace, Zeini, Miriam, Mesa-Núñez, Cristina, Thrasher, Adrian J., Bueren, Juan A., Schwartz, Jonathan D., Kohn, Donald B.

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Novel antivirals for severe enterovirus infection in immunocompromised hosts; A case series by Meinhardt, Andrea, Reilly, Liam, Kaliakatsos, Marios, Abdel-Aziz, Khaled, Alsharidah, Sondus, Bodi, Istvan, Booth, Claire, Chetty, Kritika, Evans, Jennifer, Ferreras-Antolín, Laura, Froude, Susannah, Galtrey, Clare M., Guruprasad, Suba, Hadden, Robert D., Hassell, Jane, Hyöty, Heikki, Kreins, Alexandra Y., Laiho, Jutta E., Lowe, David M., Lunn, Michael P., Mankad, Kshitij, Struik, Siske, Whittaker, Elizabeth, Worth, Austen, Yong, Patrick, Zhang, Liqun, Breuer, Judith, Kadambari, Seilesh

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Lentiviral-Mediated Ex-Vivo Gene Therapy for Pediatric Patients with Severe Leukocyte Adhesion Deficiency-I (LAD-I): Interim Results from an Ongoing Phase 1/2 Study by Booth, Claire, Sevilla, Julian, Rao, Gayatri, Lopez, Maria Chitty, Almarza, Elena, Terrazas, Dayna, Zubicaray, Josune, Gonzalez-Vicent, Marta, Chetty, Kritika, Xu-Bayford, Jinhua, O’Toole, Grainne, Fernandes, Augustine, Kuo, Caroline Y., De Oliveira, Satiro N., Mesa-Núñez, Cristina, Moore, Theodore B., Nicoletti, Eileen, Choi, Grace, Zeini, Miriam, Thrasher, Adrian J., Bueren, Juan, Schwartz, Jonathan, Kohn, Donald B.

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3 - Lentiviral-Mediated Ex-Vivo Gene Therapy for Pediatric Patients with Severe Leukocyte Adhesion Deficiency-I (LAD-I): Interim Results from an Ongoing Phase 1/2 Study by Booth, Claire, Sevilla, Julian, Rao, Gayatri, Lopez, Maria Chitty, Almarza, Elena, Terrazas, Dayna, Zubicaray, Josune, Gonzalez-Vicent, Marta, Chetty, Kritika, Xu-Bayford, Jinhua, O’Toole, Grainne, Fernandes, Augustine, Kuo, Caroline Y., De Oliveira, Satiro N., Mesa-Núñez, Cristina, Moore, Theodore B., Nicoletti, Eileen, Choi, Grace, Zeini, Miriam, Thrasher, Adrian J., Bueren, Juan, Schwartz, Jonathan, Kohn, Donald B.

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113 - Lentiviral-Mediated Gene Therapy for Patients with Fanconi Anemia [Group A]: Updated Results from Global RP-L102 Clinical Trials by Czechowicz, Agnieszka, Sevilla, Julian, Booth, Claire, Agarwal, Rajni, Zubicaray, Josune, Río, Paula, Navarro, Susana, Chetty, Kritika, O’Toole, Grainne, Xu-Bayford, Jinhua, Ancliff, Philip, Sebastián, Elena, Choi, Grace, Zeini, Miriam, Nicoletti, Eileen, Wagner, John E., Rao, Gayatri, Thrasher, Adrian J., Schwartz, Jonathan, Roncarolo, Maria Grazia, Bueren, Juan

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Lentiviral-Mediated Gene Therapy for Patients with Fanconi Anemia [Group A]: Updated Results from Global RP-L102 Clinical Trials by Czechowicz, Agnieszka, Sevilla, Julian, Booth, Claire, Agarwal, Rajni, Zubicaray, Josune, Río, Paula, Navarro, Susana, Chetty, Kritika, O’Toole, Grainne, Xu-Bayford, Jinhua, Ancliff, Philip, Sebastián, Elena, Choi, Grace, Zeini, Miriam, Nicoletti, Eileen, Wagner, John E., Rao, Gayatri, Thrasher, Adrian J., Schwartz, Jonathan, Roncarolo, Maria Grazia, Bueren, Juan

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Case report: Novel treatment regimen for enterovirus encephalitis in SCID by Chetty, Kritika, Cheng, Iek, Kaliakatsos, Marios, Gonzalez-Granado, Luis Ignacio, Klapsa, Dimitra, Martin, Javier, Bamford, Alasdair, Breuer, Judith, Booth, Claire

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