Multi-Center Clinical Trial of CAR T Cells in Pediatric/Young Adult Patients with Relapsed B-Cell ALL by Curran, Kevin J., Riviere, Isabelle, Silverman, Lewis B., Kobos, Rachel, Shukla, Neerav, Steinherz, Peter G, Boulad, Farid, Prockop, Susan, Scaradavou, Andromachi, Margossian, Steven P., Wang, Xiuyan, Wang, Yongzeng, Szenes, Victoria, Dansereau, Colleen H, MacKinnon, Brenda, Sauter, Craig S., Park, Jae H., Kernan, Nancy A., O'Reilly, Richard J, Sadelain, Michel, Brentjens, Renier J.

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Gene Therapy Using a Self-Inactivating Lentiviral Vector Improves Clinical and Laboratory Manifestations of Wiskott-Aldrich Syndrome by Chu, Julia I, Henderson, Lauren A, Armant, Myriam, Male, Frances, Dansereau, Colleen H, MacKinnon, Brenda, Burke, Christopher J, Cavanaugh, Matthew E, London, Wendy B., Barlan, Isil B, Özen, Ahmet, Baris, Safa, Karakoc-Aydiner, Elif, Kiykim, Ayça, Hanson, Imelda Celine, Despotovic, Jenny M., Saitoh, Akihiko, Takachi, Takayuki, Imai, Kohsuke, King, Alejandra, Arredondo, Silvia, Ritz, Jerome, Bushman, Frederic D, Galy, Anne, Notarangelo, Luigi Daniele, Williams, David A., Pai, Sung-Yun

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250. A Phase 2/3 Study of the Efficacy and Safety of Ex Vivo Gene Therapy with Lenti-D TM Lentiviral Vector for the Treatment of Cerebral Adrenoleukodystrophy by Eichler, Florian S., Duncan, Christine, Amartino, Hernan, Aziz-Bose, Razina, Baruchel, André, Dansereau, Colleen, Dalle, Jean-Hugues, Gaspar, H. Bobby, Gissen, Paul, Kohn, Donald B., Larghero, Jerome, Lund, Troy C., Miller, Weston P., Musolino, Patricia L., O'Meara, Tara, Orchard, Paul J., Paker, Asif M., Shah, Ami J., Shamir, Esther, Raymond, Gerald V., Sankar, Raman, Smith, Nicholas J.C., Thrasher, Adrian J., Aubourg, Patrick, Williams, David A.

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250. A Phase 2/3 Study of the Efficacy and Safety of Ex Vivo Gene Therapy with Lenti-DTM Lentiviral Vector for the Treatment of Cerebral Adrenoleukodystrophy by Eichler, Florian S., Duncan, Christine, Amartino, Hernan, Aziz-Bose, Razina, Baruchel, André, Dansereau, Colleen, Dalle, Jean-Hugues, Gaspar, H. Bobby, Gissen, Paul, Kohn, Donald B., Larghero, Jerome, Lund, Troy C., Miller, Weston P., Musolino, Patricia L., O'Meara, Tara, Orchard, Paul J., Paker, Asif M., Shah, Ami J., Shamir, Esther, Raymond, Gerald V., Sankar, Raman, Smith, Nicholas J.C., Thrasher, Adrian J., Aubourg, Patrick, Williams, David A.

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Immune Reconstitution and Preliminary Safety Analysis Of 9 Patients Treated With Somatic Gene Therapy For X-Linked Severe Combined Immunodeficiency (SCID-X1) With a Self-Inactivati... by Hacein-Bey-Abina, Salima, Pai, Sung-Yun, Bushman, Frederic, Armant, Myriam, Blanche, Stephane, Blondeau, Johanna, Caccavelli, Laure, Daley, Heather, Dansereau, Colleen, deOliveira, Satiro, Guo, Dongjing, Hopkins, Gregory, Lim, Annick, London, Wendy B., Malani, Nirav, Male, Frances, Malik, Punam, Marinovic, Maria Angelica, McDonough, Sean, Oleastro, Matias, Picard, Capucine, Ritz, Jerome, Schambach, Axel, Silberstein, Leslie E, Tsytsykova, Alla, Van der Loo, Johannes C.M., Baum, Christopher, Gaspar, H. Bobby, Kohn, Donald B., Filipovich, Alexandra H., Notarangelo, Luigi Daniele, Fischer, Alain, Cavazzana-Calvo, Marina, Williams, David A., Thrasher, Adrian J

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Lenti-D Hematopoietic Stem Cell Gene Therapy to Arrest Progression of Cerebral Adrenoleukodystrophy: Interim Results of an International Phase 2/3 Trial by Duncan, Christine, Eichler, Florian, Musolino, Patricia L., Orchard, Paul J., De Oliveira, Satiro, Thrasher, Adrian J., Armant, Myriam A., Dansereau, Colleen, Lund, Troy C., Miller, Weston P., Raymond, Gerald V., Sankar, Raman, Shah, Ami J., Sevin, Caroline, Gaspar, H. Bobby, Gissen, Paul, Amartino, Hernan, Bratkovic, Drago, Smith, Nicholas J.C., Paker, Asif M., Shamir, Esther, O'Meara, Tara, Asmal, Mohammed, Davidson, David, Aubourg, Patrick, Williams, David A.

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61 - Lenti-D Hematopoietic Stem Cell Gene Therapy to Arrest Progression of Cerebral Adrenoleukodystrophy: Interim Results of an International Phase 2/3 Trial by Duncan, Christine, Eichler, Florian, Musolino, Patricia L., Orchard, Paul J., De Oliveira, Satiro, Thrasher, Adrian J., Armant, Myriam A., Dansereau, Colleen, Lund, Troy C., Miller, Weston P., Raymond, Gerald V., Sankar, Raman, Shah, Ami J., Sevin, Caroline, Gaspar, H. Bobby, Gissen, Paul, Amartino, Hernan, Bratkovic, Drago, Smith, Nicholas J.C., Paker, Asif M., Shamir, Esther, O'Meara, Tara, Asmal, Mohammed, Davidson, David, Aubourg, Patrick, Williams, David A.

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