Intra-CSF AAV9 and AAVrh10 Administration in Nonhuman Primates: Promising Routes and Vectors for Which Neurological Diseases? by Bey, Karim, Deniaud, Johan, Dubreil, Laurence, Joussemet, Béatrice, Cristini, Joseph, Ciron, Carine, Hordeaux, Juliette, Le Boulc’h, Morwenn, Marche, Kevin, Maquigneau, Maud, Guilbaud, Michaël, Moreau, Rosalie, Larcher, Thibaut, Deschamps, Jack-Yves, Fusellier, Marion, Blouin, Véronique, Sevin, Caroline, Cartier, Nathalie, Adjali, Oumeya, Aubourg, Patrick, Moullier, Philippe, Colle, Marie-Anne

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Satellite cells fail to contribute to muscle repair but are functional in Pompe disease (glycogenosis type II) by Lagalice, Lydie, Pichon, Julien, Gougeon, Eliot, Soussi, Salwa, Deniaud, Johan, Ledevin, Mireille, Maurier, Virginie, Leroux, Isabelle, Durand, Sylvie, Ciron, Carine, Franzoso, Francesca, Dubreil, Laurence, Larcher, Thibaut, Rouger, Karl, Colle, Marie-Anne

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Efficient CNS targeting in adult mice by intrathecal infusion of single-stranded AAV9-GFP for gene therapy of neurological disorders by Bey, K, Ciron, C, Dubreil, L, Deniaud, J, Ledevin, M, Cristini, J, Blouin, V, Aubourg, P, Colle, M-A

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Efficient central nervous system AAVrh10-mediated intrathecal gene transfer in adult and neonate rats by Hordeaux, J, Dubreil, L, Deniaud, J, Iacobelli, F, Moreau, S, Ledevin, M, Le Guiner, C, Blouin, V, Le Duff, J, Mendes-Madeira, A, Rolling, F, Cherel, Y, Moullier, P, Colle, M-A

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Long-term neurologic and cardiac correction by intrathecal gene therapy in Pompe disease by Hordeaux, J, Dubreil, L, Robveille, C, Deniaud, J, Pascal, Q, Dequéant, B, Pailloux, J, Lagalice, L, Ledevin, M, Babarit, C, Costiou, P, Jamme, F, Fusellier, M, Mallem, Y, Ciron, C, Huchet, C, Caillaud, C, Colle, M-A

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Histopathologic Changes of the Ear in Canine Models of Mucopolysaccharidosis Types I and VII by Hordeaux, J., Deniaud, J., Bemelmans, I., Bertrand, L., Moreau, S., Amiaud, J., Wyers, M., Cherel, Y., Colle, M.-A.

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