THE 6-minute walk test and other endpoints in Duchenne muscular dystrophy: Longitudinal natural history observations over 48 weeks from a multicenter study by Mcdonald, Craig M., Henricson, Erik K., Abresch, R. Ted, Florence, Julaine M., Eagle, Michelle, Gappmaier, Eduard, Glanzman, Allan M., Spiegel, Robert, Barth, Jay, Elfring, Gary, Reha, Allen, Peltz, Stuart

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The 6-minute walk test and other clinical endpoints in duchenne muscular dystrophy: Reliability, concurrent validity, and minimal clinically important differences from a multicente... by McDonald, Craig M., Henricson, Erik K., Abresch, R. Ted, Florence, Julaine, Eagle, Michelle, Gappmaier, Eduard, Glanzman, Allan M., Spiegel, Robert, Barth, Jay, Elfring, Gary, Reha, Allen, Peltz, Stuart W.

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Report on the Muscular Dystrophy Campaign workshop: Exercise in neuromuscular diseases Newcastle, January 2002 by Eagle, Michelle

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Safety and efficacy of drisapersen for the treatment of Duchenne muscular dystrophy (DEMAND II): an exploratory, randomised, placebo-controlled phase 2 study by Voit, Thomas, Prof, Topaloglu, Haluk, Prof, Straub, Volker, Prof, Muntoni, Francesco, Prof, Deconinck, Nicolas, MD, Campion, Giles, MD, De Kimpe, Sjef J, PhD, Eagle, Michelle, PhD, Guglieri, Michela, MD, Hood, Steve, PhD, Liefaard, Lia, PhD, Lourbakos, Afrodite, PhD, Morgan, Allison, BSc, Nakielny, Joanna, MB, Quarcoo, Naashika, PhD, Ricotti, Valeria, MB, Rolfe, Katie, MSc, Servais, Laurent, MD, Wardell, Claire, DPhil, Wilson, Rosamund, PhD, Wright, Padraig, MD, Kraus, John E, MD

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Development of the Performance of the Upper Limb module for Duchenne muscular dystrophy by Mayhew, Anna, Mazzone, Elena S, Eagle, Michelle, Duong, Tina, Ash, Maria, Decostre, Valerie, Vandenhauwe, Marlene, Klingels, Katrijn, Florence, Julaine, Main, Marion, Bianco, Flaviana, Henrikson, Erik, Servais, Laurent, Campion, Giles, Vroom, Elizabeth, Ricotti, Valeria, Goemans, Natalie, Mcdonald, Craig, Mercuri, Eugenio

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Magnetic resonance imaging in duchenne muscular dystrophy: Longitudinal assessment of natural history over 18 months by Hollingsworth, Kieren G., Garrood, Penny, Eagle, Michelle, Bushby, Kate, Straub, Volker

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Quantitative muscle MRI as an assessment tool for monitoring disease progression in LGMD2I: a multicentre longitudinal study by Willis, Tracey A, Hollingsworth, Kieren G, Coombs, Anna, Sveen, Marie-Louise, Andersen, Søren, Stojkovic, Tanya, Eagle, Michelle, Mayhew, Anna, de Sousa, Paulo L, Dewar, Liz, Morrow, Jasper M, Sinclair, Christopher D J, Thornton, John S, Bushby, Kate, Lochmüller, Hanns, Hanna, Michael G, Hogrel, Jean-Yves, Carlier, Pierre G, Vissing, John, Straub, Volker

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Managing Duchenne muscular dystrophy – The additive effect of spinal surgery and home nocturnal ventilation in improving survival by Eagle, Michelle, Bourke, John, Bullock, Robert, Gibson, Mike, Mehta, Jwalant, Giddings, Dave, Straub, Volker, Bushby, Kate

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Quantitative magnetic resonance imaging in limb-girdle muscular dystrophy 2I: a multinational cross-sectional study by Willis, Tracey A, Hollingsworth, Kieren G, Coombs, Anna, Sveen, Marie-Louise, Andersen, Soren, Stojkovic, Tanya, Eagle, Michelle, Mayhew, Anna, de Sousa, Paulo Loureiro, Dewar, Liz, Morrow, Jasper M, Sinclair, Christopher D J, Thornton, John S, Bushby, Kate, Lochmuller, Hanns, Hanna, Michael G, Hogrel, Jean-Yves, Carlier, Pierre G, Vissing, John, Straub, Volker

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Remote Delivery of Motor Function Assessment and Training for Clinical Trials in Neuromuscular Disease: A Response to the COVID-19 Global Pandemic by James, Meredith K., Rose, Kristy, Alfano, Lindsay N., Reash, Natalie F., Eagle, Michelle, Lowes, Linda P.

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Consensus Statement on Standard of Care for Congenital Muscular Dystrophies by Wang, Ching H., Bonnemann, Carsten G., Rutkowski, Anne, Sejersen, Thomas, Bellini, Jonathan, Battista, Vanessa, Florence, Julaine M., Schara, Ulrike, Schuler, Pamela M., Wahbi, Karim, Aloysius, Annie, Bash, Robert O., Béroud, Christophe, Bertini, Enrico, Bushby, Kate, Cohn, Ronald D., Connolly, Anne M., Deconinck, Nicolas, Desguerre, Isabelle, Eagle, Michelle, Estournet-Mathiaud, Brigitte, Ferreiro, Ana, Fujak, Albert, Goemans, Nathalie, Iannaccone, Susan T., Jouinot, Patricia, Main, Marion, Melacini, Paola, Mueller-Felber, Wolfgang, Muntoni, Francesco, Nelson, Leslie L., Rahbek, Jes, Quijano-Roy, Susana, Sewry, Caroline, Storhaug, Kari, Simonds, Anita, Tseng, Brian, Vajsar, Jiri, Vianello, Andrea, Zeller, Reinhard

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Aquatic therapy for children with Duchenne muscular dystrophy: a pilot feasibility randomised controlled trial and mixed-methods process evaluation by Hind, Daniel, Parkin, James, Whitworth, Victoria, Rex, Saleema, Young, Tracey, Hampson, Lisa, Sheehan, Jennie, Maguire, Chin, Cantrill, Hannah, Scott, Elaine, Epps, Heather, Main, Marion, Geary, Michelle, McMurchie, Heather, Pallant, Lindsey, Woods, Daniel, Freeman, Jennifer, Lee, Ellen, Eagle, Michelle, Willis, Tracey, Muntoni, Francesco, Baxter, Peter

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Consensus Guidelines for Improving Quality of Assessment and Training for Neuromuscular Diseases by Duong, Tina, Krosschell, Kristin J, James, Meredith K, Nelson, Leslie, Alfano, Lindsay N, Eichinger, Katy, Mazzone, Elena, Rose, Kristy, Lowes, Linda P, Mayhew, Anna, Florence, Julaine, King, Wendy, Senesac, Claudia R, Eagle, Michelle

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Mesenchymal Lineage Stem Cells Have Pronounced Anti‐Inflammatory Effects in the Twitcher Mouse Model of Krabbe's Disease by Ripoll, Cynthia B., Flaat, Mette, Klopf‐Eiermann, Jessica, Fisher‐Perkins, Jeanne M., Trygg, Cynthia B., Scruggs, Brittni A., McCants, Marjorie L., Leonard, Helen Paige, Lin, Amy F., Zhang, Shijia, Eagle, Michelle E., Alvarez, Xavier, Li, Yu Teh, Li, Su Chen, Gimble, Jeffrey M., Bunnell, Bruce A.

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One Year Outcome of Boys With Duchenne Muscular Dystrophy Using the Bayley-III Scales of Infant and Toddler Development by Connolly, Anne M., MD, Florence, Julaine M., PT, DPT, Cradock, Mary M., PHD, Eagle, Michelle, PhD, MSc, MCSP, Flanigan, Kevin M., MD, McDonald, Craig M., MD, Karachunski, Peter I., MD, Darras, Basil T., MD, Bushby, Kate, MD, Malkus, Elizabeth C., PT, MHS, Golumbek, Paul T., MD, PhD, Zaidman, Craig M., MD, Miller, J. Philip, PhD, Mendell, Jerry R., MD

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Natural history of limb girdle muscular dystrophy R9 over 6 years: searching for trial endpoints by Murphy, Alexander P., Morrow, Jasper, Dahlqvist, Julia R., Stojkovic, Tanya, Willis, Tracey A., Sinclair, Christopher D. J., Wastling, Stephen, Yousry, Tarek, Hanna, Michael S., James, Meredith K., Mayhew, Anna, Eagle, Michelle, Lee, Laurence E., Hogrel, Jean‐Yves, Carlier, Pierre G., Thornton, John S., Vissing, John, Hollingsworth, Kieren G., Straub, Volker

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Correction of neuromuscular scoliosis in patients with preexisting respiratory failure by GILL, Inder, EAGLE, Michelle, MEHTA, Jwalant S, GIBSON, Michael J, BUSHBY, K, BULLOCK, R

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Cardiac and respiratory failure in limb-girdle muscular dystrophy 2I by Poppe, Maja, Bourke, John, Eagle, Michelle, Frosk, Patrick, Wrogemann, Klaus, Greenberg, Cheryl, Muntoni, Francesco, Voit, Thomas, Straub, Volker, Hilton-Jones, David, Shirodaria, Cheerag, Bushby, Kate

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Aquatic therapy for boys with Duchenne muscular dystrophy (DMD): an external pilot randomised controlled trial by Hind, Daniel, Parkin, James, Whitworth, Victoria, Rex, Saleema, Young, Tracey, Hampson, Lisa, Sheehan, Jennie, Maguire, Chin, Cantrill, Hannah, Scott, Elaine, Epps, Heather, Main, Marion, Geary, Michelle, McMurchie, Heather, Pallant, Lindsey, Woods, Daniel, Freeman, Jennifer, Lee, Ellen, Eagle, Michelle, Willis, Tracey, Muntoni, Francesco, Baxter, Peter

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Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial by McDonald, Craig M, Campbell, Craig, Torricelli, Ricardo Erazo, Finkel, Richard S, Flanigan, Kevin M, Goemans, Nathalie, Heydemann, Peter, Kaminska, Anna, Kirschner, Janbernd, Muntoni, Francesco, Osorio, Andrés Nascimento, Schara, Ulrike, Sejersen, Thomas, Shieh, Perry B, Sweeney, H Lee, Topaloglu, Haluk, Tulinius, Már, Vilchez, Juan J, Voit, Thomas, Wong, Brenda, Elfring, Gary, Kroger, Hans, Luo, Xiaohui, McIntosh, Joseph, Ong, Tuyen, Riebling, Peter, Souza, Marcio, Spiegel, Robert J, Peltz, Stuart W, Mercuri, Eugenio, Alfano, Lindsay N, Eagle, Michelle, James, Meredith K, Lowes, Linda, Mayhew, Anna, Mazzone, Elena S, Nelson, Leslie, Rose, Kristy J, Abdel-Hamid, Hoda Z, Apkon, Susan D, Barohn, Richard J, Bertini, Enrico, Bloetzer, Clemens, de Vaud, Lausanne Canton, Butterfield, Russell J, Chabrol, Brigitte, Chae, Jong-Hee, Jongno-gu, Daehak-ro, Comi, Giacomi Pietro, Darras, Basil T, Dastgir, Jahannaz, Desguerre, Isabelle, Escobar, Raul G, Finanger, Erika, Guglieri, Michela, Hughes, Imelda, Iannaccone, Susan T, Jones, Kristi J, Karachunski, Peter, Kudr, Martin, Lotze, Timothy, Mah, Jean K, Mathews, Katherine, Nevo, Yoram, Parsons, Julie, Péréon, Yann, de Queiroz Campos Araujo, Alexandra Prufer, Renfroe, J Ben, de Resende, Maria Bernadete Dutra, Ryan, Monique, Selby, Kathryn, Tennekoon, Gihan, Vita, Giuseppe

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