G.P.104 by Naryshkin, N.A, Dakka, A, Gabbeta, V, Pichardo, J, Woll, M.G, Zhang, N, Karp, G.M, Welch, E.M

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Small molecule compounds that promote exon skipping in the DMD gene by Naryshkin, N, Dakka, A, Gabbeta, V, Pichardo, J, Vazirani, P, Ryan, G, Woll, M, Turpoff, A, Zhang, N, Zhang, S, Karp, G, Welch, E

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T.P.7 Small molecule compounds correct alternative splicing of the SMN2 gene and restore SMN protein expression and function by Naryshkin, N, Narasimhan, J, Dakka, A, Gabbeta, V, Haley, M, Jung, S, Crona, J, Vazirani, P, Furia, B, Qi, H, Woll, M, Lee, S, Choi, S, Koyama, H, Yang, T, Chen, G, Zhang, S, Zhang, N, Huang, S, Li, C, Turpoff, A, Hedrick, J, Zhao, X, Mollin, A, Zadel, M, Letinski, S, Paushkin, S, Kobayashi, D, McCarthy, K, Chen, K, Metzger, F, Ratni, H, Gerlach, I, Khwaja, O, Trifillis, P, Colacino, J, Babiak, J, Almstead, N, Peltz, S, Karp, G, Weetall, M, Welch, E

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P3.12 Small molecule compounds that correct alternative splicing of the SMN2 gene and restore SMN protein expression and function by Naryshkin, N.A, Narasimhan, J, Dakka, A, Gabbeta, V, Haley, M, Crona, J, Jung, S, Vazirani, P, Furia, B, Qi, H, Woll, M, Yang, T, Lee, S, Choi, S, Chen, G, Zhang, S, Zhang, N, Huang, S, Li, C, Turpoff, A, Hedrick, J, Zhao, X, Mollin, A, Letinski, S, Risher, N, Paushkin, S, Kobayashi, D, McCarthy, K, Pleiss, M, Chen, K, Almstead, N, Colacino, J, Babiak, J, Peltz, S, Karp, G, Weetall, M, Welch, E.M

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G.P.104: Oral small molecule compounds that promote the skipping of exon 51 in the DMD gene by Naryshkin, N.A., Dakka, A., Gabbeta, V., Pichardo, J., Woll, M.G., Zhang, N., Karp, G.M., Welch, E.M.

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G.P.250 - Small molecule compounds that promote exon skipping in the DMD gene by Naryshkin, N., Dakka, A., Gabbeta, V., Pichardo, J., Vazirani, P., Ryan, G., Woll, M., Turpoff, A., Zhang, N., Zhang, S., Karp, G., Welch, E.

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Differential Binding of an SRF/NK-2/MEF2 Transcription Factor Complex in Normal Versus Neoplastic Smooth Muscle Tissues by Phiel, Christopher J., Gabbeta, Vijayalakshmi, Parsons, Linda M., Rothblat, David, Harvey, Richard P., McHugh, Kirk M.

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Isolation and characterization of a novel short chain alcohol dehydrogenase-like isozyme by differential display of distinct smooth muscle cell phenotypes by Trzyna, Wendy C., Gabbeta, Vijayalakshmi, McHugh, Kirk M.

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SMN2 splicing modifiers improve motor function and longevity in mice with spinal muscular atrophy by Naryshkin, Nikolai A., Weetall, Marla, Dakka, Amal, Narasimhan, Jana, Zhao, Xin, Feng, Zhihua, Ling, Karen K. Y., Karp, Gary M., Qi, Hongyan, Woll, Matthew G., Chen, Guangming, Zhang, Nanjing, Gabbeta, Vijayalakshmi, Vazirani, Priya, Bhattacharyya, Anuradha, Furia, Bansri, Risher, Nicole, Sheedy, Josephine, Kong, Ronald, Ma, Jiyuan, Turpoff, Anthony, Lee, Chang-Sun, Zhang, Xiaoyan, Moon, Young-Choon, Trifillis, Panayiota, Welch, Ellen M., Colacino, Joseph M., Babiak, John, Almstead, Neil G., Peltz, Stuart W., Eng, Loren A., Chen, Karen S., Mull, Jesse L., Lynes, Maureen S., Rubin, Lee L., Fontoura, Paulo, Santarelli, Luca, Haehnke, Daniel, McCarthy, Kathleen D., Schmucki, Roland, Ebeling, Martin, Sivaramakrishnan, Manaswini, Ko, Chien-Ping, Paushkin, Sergey V., Ratni, Hasane, Gerlach, Irene, Ghosh, Anirvan, Metzger, Friedrich

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Motor neuron disease. SMN2 splicing modifiers improve motor function and longevity in mice with spinal muscular atrophy by Naryshkin, Nikolai A, Weetall, Marla, Dakka, Amal, Narasimhan, Jana, Zhao, Xin, Feng, Zhihua, Ling, Karen K Y, Karp, Gary M, Qi, Hongyan, Woll, Matthew G, Chen, Guangming, Zhang, Nanjing, Gabbeta, Vijayalakshmi, Vazirani, Priya, Bhattacharyya, Anuradha, Furia, Bansri, Risher, Nicole, Sheedy, Josephine, Kong, Ronald, Ma, Jiyuan, Turpoff, Anthony, Lee, Chang-Sun, Zhang, Xiaoyan, Moon, Young-Choon, Trifillis, Panayiota, Welch, Ellen M, Colacino, Joseph M, Babiak, John, Almstead, Neil G, Peltz, Stuart W, Eng, Loren A, Chen, Karen S, Mull, Jesse L, Lynes, Maureen S, Rubin, Lee L, Fontoura, Paulo, Santarelli, Luca, Haehnke, Daniel, McCarthy, Kathleen D, Schmucki, Roland, Ebeling, Martin, Sivaramakrishnan, Manaswini, Ko, Chien-Ping, Paushkin, Sergey V, Ratni, Hasane, Gerlach, Irene, Ghosh, Anirvan, Metzger, Friedrich

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