Marfan syndrome in adolescence: adolescents’ perspectives on (physical) functioning, disability, contextual factors and support needs by Warnink-Kavelaars, Jessica, Beelen, Anita, Goedhart, Tine M. H. J., de Koning, Lisanne E., Nollet, Frans, Alsem, Mattijs W., Menke, Leonie A., Engelbert, Raoul H. H.

Get full text

The road to implementation of pharmacokinetic-guided dosing of factor replacement therapy in hemophilia and allied bleeding disorders. Identifying knowledge gaps by mapping barrier... by Goedhart, Tine M.H.J., Janssen, A., Mathôt, Ron A.A., Cnossen, Marjon H.

Get full text

A new population pharmacokinetic model for recombinant factor IX‐Fc fusion concentrate including young children with haemophilia B by Koopman, Sjoerd F., Goedhart, Tine M.H.J., Bukkems, Laura H., Mulders, Trevor M., Leebeek, Frank W.G., Fijnvandraat, Karin, Coppens, Michiel, Mathias, Mary, Collins, Peter W., Tait, R. Campbell, Bagot, Catherine N., Curry, Nicola, Payne, Jeanette, Chowdary, Pratima, Cnossen, Marjon H., Mathôt, Ron A.A.

Get full text

Does difference between label and actual potency of factor VIII concentrate affect pharmacokinetic‐guided dosing of replacement therapy in haemophilia A? by Goedhart, Tine M.H.J., Bukkems, Laura H., Moort, Iris, Spence, Colin C., Zwaan, Michel C., Maat, Moniek P.M., Mathôt, Ron A.A., Cnossen, Marjon H.

Get full text

Predictive performance of pharmacokinetic-guided prophylactic dosing of factor concentrates in hemophilia A and B by Goedhart, Tine M.H.J., Bukkems, Laura H., Zwagemaker, Anne-Fleur, Coppens, Michiel, Fijnvandraat, Karin, Schols, Saskia E.M., Schutgens, Roger E.G., Eikenboom, Jeroen, Heubel-Moenen, Floor C.J.I., Ypma, Paula F., Nieuwenhuizen, Laurens, Meijer, Karina, Leebeek, Frank W.G., Mathôt, Ron A.A., Cnossen, Marjon H.

Get full text

Population pharmacokinetic modeling of factor concentrates in hemophilia: an overview and evaluation of best practice by Goedhart, Tine M.H.J., Bukkems, Laura H., Zwaan, C. Michel, Mathôt, Ron A.A., Cnossen, Marjon H.

Get full text

Design of a Prospective Study on Pharmacokinetic-Guided Dosing of Prophylactic Factor Replacement in Hemophilia A and B (OPTI-CLOT TARGET Study) by Goedhart, Tine M.H.J., Bukkems, Laura H., Coppens, Michiel, Fijnvandraat, Karin J., Schols, Saskia E.M., Schutgens, Roger E.G., Eikenboom, Jeroen, Heubel-Moenen, Floor C.J.I., Ypma, Paula F., Nieuwenhuizen, L., Meijer, K., Leebeek, Frank W. G., Mathôt, Ron A.A., Cnossen, Marjon H.

Get full text