Inclusion of a short hairpin RNA targeting BCL11A into a β-globin expressing vector allows concurrent synthesis of curative adult and fetal hemoglobin by Pires Lourenco, Silvia, Jarocha, Danuta, Ghiaccio, Valentina, Guerra, Amaliris, Abdulmalik, Osheiza, La, Ping, Zezulin, Alexandra, Smith-Whitley, Kim, Kwiatkowski, Janet L., Guzikowski, Virginia, Nakamura, Yukio, Raabe, Tobias, Breda, Laura, Rivella, Stefano

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Preclinical Evaluation of ALS20, a New and Improved Lentiviral Vector for Beta-Globinopathies by Breda, Laura, Ghiaccio, Valentina, Pires Lourenco, Silvia, Jarocha, Danuta Jadwiga, Ikawa, Yasuhiro, Tanaka, Naoto, Guzikowski, Virginia, Casu, Carla, Smith-Whitley, Kim, Kwiatkowski, Janet L., Rivella, Stefano

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Inclusion of a short hairpin RNA targeting BCL11A into a b-globin expressing vector allows concurrent synthesis of curative adult and fetal hemoglobin by Lourenco, Silvia Pires, Jarocha, Danuta, Ghiaccio, Valentina, Guerra, Amaliris, Abdulmalik, Osheiza, La, Ping, Zezulin, Alexandra, Smith-Whitley, Kim, Kwiatkowski, Janet L., Guzikowski, Virginia, Nakamura, Yukio, Raabe, Tobias, Breda, Laura, Rivella, Stefano

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Lentiviral vector ALS20 yields high hemoglobin levels with low genomic integrations for treatment of beta-globinopathies by Breda, Laura, Ghiaccio, Valentina, Tanaka, Naoto, Jarocha, Danuta, Ikawa, Yasuhiro, Abdulmalik, Osheiza, Dong, Alisa, Casu, Carla, Raabe, Tobias D., Shan, Xiaochuan, Danet-Desnoyers, Gwenn A., Doto, Aoife M., Everett, John, Bushman, Frederic D., Radaelli, Enrico, Assenmacher, Charles A., Tarrant, James C., Hoepp, Natalie, Kurita, Ryo, Nakamura, Yukio, Guzikowski, Virginia, Smith-Whitley, Kim, Kwiatkowski, Janet L., Rivella, Stefano

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Improved Lentiviral Vectors for the Cure of Hemoglobinopathies by Breda, Laura, Ghiaccio, Valentina, Zaidi, Hanyia, Pires Lourenco, Silvia, Casu, Carla, Smith-Whitley, Kim, Kwiatkowski, Janet L., Carrion, Vanessa, Guzikowski, Virginia, Kurita, Ryo, Nakamura, Yukio, Rivella, Stefano

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Solid organ transplants following hematopoietic stem cell transplant in children by Bunin, Nancy, Guzikowski, Virginia, Rand, Elizabeth R., Goldfarb, Samuel, Baluarte, Jorge, Meyers, Kevin, Olthoff, Kim M.

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Solid organ transplants following hematopoietic stem cell transplant in children: SOT following HSCT in children by Bunin, Nancy, Guzikowski, Virginia, Rand, Elizabeth R., Goldfarb, Samuel, Baluarte, Jorge, Meyers, Kevin, Olthoff, Kim M.

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