Gene therapy mediated correction of neurological manifestations of MPS IIIC using a novel AAV serotype by O'Leary, Claire, Antunes, Andre, Tordo, Julie, Liao, Ai Yin, Parker, Helen, Gleitz, Helene, Holley, Rebecca, Youshani, Amir Saam, Dridi, Larbi, Martins, Carla, Pshezhetsky, Alexey, Henckearts, Els, Bigger, Brian

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