FSHD / OPMD / EDMD / DMI by Statland, J., Bravver, E., Karam, C., Elman, L., Johnson, N., Joyce, N., Kissel, J., Shieh, P., Korngut, L., Weihl, C., Tawil, R., Amato, A., Campbell, C., Genge, A., Manousakis, G., Leneus, A., Miller, B., Sherman, M., Glasser, C., Attie, K.

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FSHD / OPMD / EDMD / DMI: P.365Results for a dose-escalation phase 2 study to evaluate ACE-083, a local muscle therapeutic, in patients with facioscapulohumeral muscular dystrophy by Statland, J., Bravver, E., Karam, C., Elman, L., Johnson, N., Joyce, N., Kissel, J., Shieh, P., Korngut, L., Weihl, C., Tawil, R., Amato, A., Campbell, C., Genge, A., Manousakis, G., Leneus, A., Miller, B., Sherman, M., Glasser, C., Attie, K.

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Randomized phase 2 study of ACE‐083, a muscle‐promoting agent, in facioscapulohumeral muscular dystrophy by Statland, Jeffrey M., Campbell, Craig, Desai, Urvi, Karam, Chafic, Díaz‐Manera, Jordi, Guptill, Jeffrey T., Korngut, Lawrence, Genge, Angela, Tawil, Rabi N., Elman, Lauren, Joyce, Nanette C., Wagner, Kathryn R., Manousakis, Georgios, Amato, Anthony A., Butterfield, Russell J., Shieh, Perry B., Wicklund, Matthew, Gamez, Josep, Bodkin, Cynthia, Pestronk, Alan, Weihl, Conrad C., Vilchez‐Padilla, Juan J., Johnson, Nicholas E., Mathews, Katherine D., Miller, Barry, Leneus, Ashley, Fowler, Marcie, Rijn, Marc, Attie, Kenneth M.

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Luspatercept Increases Hemoglobin, Decreases Transfusion Burden and Improves Iron Overload in Adults with Beta-Thalassemia by Piga, Antonio G., Tartaglione, Immacolata, Gamberini, Rita, Voskaridou, Ersi, Melpignano, Angela, Ricchi, Paolo, Caruso, Vincenzo, Pietrangelo, Antonello, Zhang, Xiaosha, Wilson, Dawn M., Leneus, Ashley, Laadem, Abderrahmane, Sherman, Matthew L., Attie, Kenneth M.

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