Laryngeal, Tracheal, and Bronchial Disease in the Mucopolysaccharidoses: Endoscopic Study by Pires de Mello, Paulo, Lopes Barth, Anneliese, de Araujo Torres, Danielle, Pires de Mello Valente, Mariana, Dain Gandelman Horovitz, Dafne

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Alternative laronidase dose regimen for patients with mucopolysaccharidosis I: a multinational, retrospective, chart review case series by Horovitz, Dafne Dain Gandelman, Acosta, Angelina X, Giugliani, Roberto, Hlavatá, Anna, Hlavatá, Katarína, Tchan, Michel C, Lopes Barth, Anneliese, Cardoso, Jr, Laercio, Embiruçu de Araújo Leão, Emília Katiane, Esposito, Ana Carolina, Kyosen, Sandra Obikawa, De Souza, Carolina Fischinger Moura, Martins, Ana Maria

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Mucopolysaccharidosis Type I by Kubaski, Francyne, de Oliveira Poswar, Fabiano, Michelin-Tirelli, Kristiane, Matte, Ursula da Silveira, Horovitz, Dafne D, Barth, Anneliese Lopes, Baldo, Guilherme, Vairo, Filippo, Giugliani, Roberto

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Otolaryngologists and the Early Diagnosis of Mucopolysaccharidoses: A Cross-Sectional Study by Torres, Danielle de Araujo, Barth, Anneliese Lopes, Valente, Mariana Pires de Mello, Mello, Paulo Pires de, Horovitz, Dafne Dain Gandelman

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Need leads to change: Transition to home infusion in Pompe disease in Brazil in the COVID-19 pandemic by Horovitz, Dafne Dain Gandelman, Barth, Anneliese Lopes, Alves, Welton Correia, Llerena, Juan Clinton

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Early enzyme replacement therapy in a CRIM positive classic infantile Pompe patient: 11-year follow-up of a still progressive disease by Barth, Anneliese Lopes, de Menezes, Livia Almeida, Nehab, Marcio, Meirelles, Antonio Flávio Vitarelli, Canedo, Nathalie Henriques Silva, Horovitz, Dafne Dain Gandelman, Llerena, Juan Clinton

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Mucopolysaccharidosis VII in Brazil: natural history and clinical findings by Giugliani, Roberto, Barth, Anneliese Lopes, Dumas, Melissa Rossi Calvão, da Silva Franco, José Francisco, de Rosso Giuliani, Liane, Grangeiro, Carlos Henrique Paiva, Horovitz, Dafne Dain Gandelman, Kim, Chong Ae, de Araújo Leão, Emilia Katiane Embiruçu, de Medeiros, Paula Frassinetti Vasconcelos, Miguel, Diego Santana Chaves Geraldo, Moreira, Maria Espírito Santo Almeida, dos Santos, Helena Maria Guimarães Pimentel, da Silva, Luiz Carlos Santana, da Silva, Luiz Roberto, de Souza, Isabel Neves, Nalin, Tatiele, Garcia, Daniel

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Spinal cord occupation ratio (SCOR) and its application in the diagnosis of cervical spinal cord compression in Mucopolysaccharidoses by Almeida, Julia Valeriano de, Barth, Anneliese Lopes, Costa, Alessandra Augusta Penna e, Horovitz, Dafne Dain Gandelman

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Alternative laronidase dose regimen for patients with mucopolysaccharidosis i by Martins, Ana M., Acosta, Angelina X., Giugliani, Roberto, Hlavatá, Anna, Hlavatá, Katarina, Tchan, Michel C., Barth, Anneliese Lopes, Cardoso, Laercio, de Araújo Leão, Emilia Katiane Embiruçu, Esposito, Ana Carolina, Kyosen, Sandra Obikawa, De Souza, Carolina Fischinger Moura, Horovitz, Dafne Dain Gandelman

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Oral and craniofacial manifestations in a Hunter syndrome patient with hematopoietic stem cell transplantation: A case report by Torres, Rafaela de Oliveira, Pintor, Andréa Vaz Braga, Guedes, Fábio Ribeiro, Freitas‐Fernandes, Liana Bastos, Barth, Anneliese Lopes, Horovitz, Dafne Dain Gandelman, Souza, Ivete Pomarico Ribeiro

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