268 Virus-like particle–mediated Cas9/gRNA delivery with a CFTR super exon rescues CFTR function in differentiated primary human bronchial epithelial cells by Aspiras, A., Bell, A., Misiolek, R. Valdez, Yan, K., Macadino, C., Bukis, K., Coote, K., Mense, M., Cotton, C., Valley, H.

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257 Evaluating genetic components to move toward a highly effective CFTR super exon by Yan, K., Bell, A., Macadino, C., Conte, J., Armstrong, M., Cheng, Y., Coote, K., Allaire, N., Sivachenko, A., Mense, M., Cotton, C., Valley, H.

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261 Optimized CFTR E2-27 super exon cargos rescue CFTR function by Yan, K., Macadino, C., Bukis, K., Bell, A., Chado, M., Armstrong, M., Conte, J., Cheng, Y., Tabak, B., Coote, K., Allaire, N., Sivachenko, A., Mense, M., Cotton, C., Valley, H.

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663 Modulation of cystic fibrosis transmembrane conductance regulator intron 22 alternative polyadenylation use may have therapeutic potential for the treatment of certain 3′ cysti... by Allaire, N., Yoon, J., Armstrong, M., Valley, H., Macadino, C., Sivachenko, A., Conte, J., Tabak, B., Bihler, H., Cheng, Y., Coote, K., Cotton, C., Mense, M.

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