Search Results - McPhee, Scott W.J.

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  1. 1
    Long-term follow-up after gene therapy for canavan disease

    Long-term follow-up after gene therapy for canavan disease by Leone, Paola, Shera, David, McPhee, Scott W J, Francis, Jeremy S, Kolodny, Edwin H, Bilaniuk, Larissa T, Wang, Dah-Jyuu, Assadi, Mitra, Goldfarb, Olga, Goldman, H Warren, Freese, Andrew, Young, Deborah, During, Matthew J, Samulski, R Jude, Janson, Christopher G

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  2. 2
    BAX 335 hemophilia B gene therapy clinical trial results: potential impact of CpG sequences on gene expression

    BAX 335 hemophilia B gene therapy clinical trial results: potential impact of CpG sequences on gene expression by Konkle, Barbara A., Walsh, Christopher E., Escobar, Miguel A., Josephson, Neil C., Young, Guy, von Drygalski, Annette, McPhee, Scott W.J., Samulski, R. Jude, Bilic, Ivan, de la Rosa, Maurus, Reipert, Birgit M., Rottensteiner, Hanspeter, Scheiflinger, Friedrich, Chapin, John C., Ewenstein, Bruce, Monahan, Paul E.

    Published in Blood
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  3. 3
    Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector

    Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector by Bowles, Dawn E, McPhee, Scott WJ, Li, Chengwen, Gray, Steven J, Samulski, Jade J, Camp, Angelique S, Li, Juan, Wang, Bing, Monahan, Paul E, Rabinowitz, Joseph E, Grieger, Joshua C, Govindasamy, Lakshmanan, Agbandje-McKenna, Mavis, Xiao, Xiao, Samulski, R Jude

    Published in Molecular therapy
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  4. 4
    Viral-based gene transfer to the mammalian CNS for functional genomic studies

    Viral-based gene transfer to the mammalian CNS for functional genomic studies by Janson, Christopher G., McPhee, Scott W.J., Leone, Paola, Freese, Andrew, During, Matthew J.

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