Search Results - Nalysnyk, Lubomyra

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  1. 1
    Natural history of acid sphingomyelinase deficiency (ASMD) among European patients during childhood and adolescence: A retrospective observational study

    Natural history of acid sphingomyelinase deficiency (ASMD) among European patients during childhood and adolescence: A retrospective observational study by Mengel, Eugen, Scarpa, Maurizio, Guffon, Nathalie, Jones, Simon A., Goriya, Vishal, Msihid, Jerome, Dyevre, Valérie, Rodriguez, Carly, Gasparic, Maja, Nalysnyk, Lubomyra, Laredo, Fernando, Pulikottil-Jacob, Ruth

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  2. 2
    Clinical relevance of endpoints in clinical trials for acid sphingomyelinase deficiency enzyme replacement therapy

    Clinical relevance of endpoints in clinical trials for acid sphingomyelinase deficiency enzyme replacement therapy by Jones, Simon A., McGovern, Margaret, Lidove, Olivier, Giugliani, Roberto, Mistry, Pramod K., Dionisi-Vici, Carlo, Munoz-Rojas, Maria-Veronica, Nalysnyk, Lubomyra, Schecter, Alison D., Wasserstein, Melissa

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  3. 3
    A conceptual framework of patient-reported outcomes for type 3 Gaucher disease

    A conceptual framework of patient-reported outcomes for type 3 Gaucher disease by Hamed, Alaa, Nalysnyk, Lubomyra, Tilimo, Milki, Krupnick, Robert, Gee, Alex

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  4. 4
    Natural history of acid sphingomyelinase deficiency among European patients during childhood and adolescence: A retrospective observational study

    Natural history of acid sphingomyelinase deficiency among European patients during childhood and adolescence: A retrospective observational study by Mengel, Eugen, Scarpa, Maurizio, Guffon, Nathalie, Jones, Simon A., Goriya, Vishal, Msihid, Jérôme, Dyevre, Valerie, Rodriguez, Carly, Gasparic, Maja, Nalysnyk, Lubomyra, Laredo, Fernando, Pulikottil-Jacob, Ruth

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  5. 5
    Impact of Potential Symptoms and Risks Associated with Acid Sphingomyelinase Deficiency on Patients and Caregivers: A Best-Worst Scaling Study

    Impact of Potential Symptoms and Risks Associated with Acid Sphingomyelinase Deficiency on Patients and Caregivers: A Best-Worst Scaling Study by Mansfield, Carol, Nalysnyk, Lubomyra, Joshi, Dhaivat, Coulter, Joshua, Pulikottil-Jacob, Ruth

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  6. 6
    Imiglucerase Treatment Associated with Reduction of Bone Claims in Gaucher Patients: Analysis of US Claims Data

    Imiglucerase Treatment Associated with Reduction of Bone Claims in Gaucher Patients: Analysis of US Claims Data by Nalysnyk, Lubomyra, Selzer, Martin, Hamed, Alaa, Weinreb, Neal J.

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