Evaluation of Therapeutic Oligonucleotides for Familial Amyloid Polyneuropathy in Patient-Derived Hepatocyte-Like Cells by Niemietz, Christoph J, Sauer, Vanessa, Stella, Jacqueline, Fleischhauer, Lutz, Chandhok, Gursimran, Guttmann, Sarah, Avsar, Yesim, Guo, Shuling, Ackermann, Elizabeth J, Gollob, Jared, Monia, Brett P, Zibert, Andree, Schmidt, Hartmut H-J

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In Vitro and In Vivo Effects of SerpinA1 on the Modulation of Transthyretin Proteolysis by Bezerra, Filipa, Niemietz, Christoph, Schmidt, Hartmut H. J., Zibert, Andree, Guo, Shuling, Monia, Brett P., Gonçalves, Paula, Saraiva, Maria João, Almeida, Maria Rosário

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Methanobactin reverses acute liver failure in a rat model of Wilson disease by Lichtmannegger, Josef, Leitzinger, Christin, Wimmer, Ralf, Schmitt, Sabine, Schulz, Sabine, Kabiri, Yaschar, Eberhagen, Carola, Rieder, Tamara, Janik, Dirk, Neff, Frauke, Straub, Beate K, Schirmacher, Peter, DiSpirito, Alan A, Bandow, Nathan, Baral, Bipin S, Flatley, Andrew, Kremmer, Elisabeth, Denk, Gerald, Reiter, Florian P, Hohenester, Simon, Eckardt-Schupp, Friedericke, Dencher, Norbert A, Adamski, Jerzy, Sauer, Vanessa, Niemietz, Christoph, Schmidt, Hartmut H J, Merle, Uta, Gotthardt, Daniel Nils, Kroemer, Guido, Weiss, Karl Heinz, Zischka, Hans

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SERPINA1 modulates expression of amyloidogenic transthyretin by Niemietz, Christoph, Bezerra, Filipa, Almeida, Maria Rosário, Guo, Shuling, Monia, Brett P., Saraiva, Maria João, Schütz, Paula, Schmidt, Hartmut H.-J., Zibert, Andree

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APOE polymorphism in ATTR amyloidosis patients treated with lipid nanoparticle siRNA by Niemietz, Christoph, Nadzemova, Oksana, Zibert, Andree, Schmidt, Hartmut H.-J.

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In vitro and in vivo effects of SerpinA1 on the modulation of Transthyretin proteolysis by Bezerra, Filipa, Niemietz, Christoph, Schmidt, Hartmut H. J., Zibert, Andree, Guo, Shuling, Monia, Brett P., Gonçalves, Paula Isabel Meira, Saraiva, Maria João, Almeida, Maria Rosário

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