Search Results - Osmon, Karlaina J.L.

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  1. 1
    Intrathecal delivery of a bicistronic AAV9 vector expressing β-hexosaminidase A corrects Sandhoff disease in a murine model: A dosage study

    Intrathecal delivery of a bicistronic AAV9 vector expressing β-hexosaminidase A corrects Sandhoff disease in a murine model: A dosage study by Ryckman, Alex E., Deschenes, Natalie M., Quinville, Brianna M., Osmon, Karlaina J.L., Mitchell, Melissa, Chen, Zhilin, Gray, Steven J., Walia, Jagdeep S.

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  2. 2
    Efficacy of a Bicistronic Vector for Correction of Sandhoff Disease in a Mouse Model

    Efficacy of a Bicistronic Vector for Correction of Sandhoff Disease in a Mouse Model by Woodley, Evan, Osmon, Karlaina J L, Thompson, Patrick, Richmond, Christopher, Chen, Zhilin, Gray, Steven J, Walia, Jagdeep S

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  3. 3
    Efficacy of Adeno-Associated Virus Serotype 9-Mediated Gene Therapy for AB-Variant GM2 Gangliosidosis

    Efficacy of Adeno-Associated Virus Serotype 9-Mediated Gene Therapy for AB-Variant GM2 Gangliosidosis by Vyas, Meera, Deschenes, Natalie M, Osmon, Karlaina J. L, Chen, Zhilin, Ahmad, Imtiaz, Kot, Shalini, Thompson, Patrick, Richmond, Chris, Gray, Steven J, Walia, Jagdeep S

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  4. 4
    Battery of Behavioral Tests Assessing General Locomotion, Muscular Strength, and Coordination in Mice

    Battery of Behavioral Tests Assessing General Locomotion, Muscular Strength, and Coordination in Mice by Osmon, Karlaina Jl, Vyas, Meera, Woodley, Evan, Thompson, Patrick, Walia, Jagdeep S

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  5. 5
    363. Improvement of Sandhoff Phenotype Following Intravenous Injection of Adeno-Associated Viral Vector Expressing a Hexosaminidase Isoenzyme in Adult Sandhoff Mice: Preclinical Safety and Efficacy Study

    363. Improvement of Sandhoff Phenotype Following Intravenous Injection of Adeno-Associated Viral Vector Expressing a Hexosaminidase Isoenzyme in Adult Sandhoff Mice: Preclinical Sa... by Osmon, Karlaina J.L., Woodley, Evan, Thompson, Patrick, Karumuthil-Melethil, Subha, Gray, Steven, Walia, Jagdeep

    Published in Molecular therapy
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  6. 6
    711. Intravenous Neonatal Gene Therapy Corrects GM2 Gangliosidosis in Sandhoff Mice for Long-Term, By Using AAV Viral Vector Expressing a New Hexosaminidase Variant

    711. Intravenous Neonatal Gene Therapy Corrects GM2 Gangliosidosis in Sandhoff Mice for Long-Term, By Using AAV Viral Vector Expressing a New Hexosaminidase Variant by Osmon, Karlaina J.L., Woodley, Evan, Thompson, Patrick, Ong, Katalina, Karumuthil-Melethil, Subha, Mark, Brian, Mahuran, Don, Gray, Steven J., Walia, Jagdeep S.

    Published in Molecular therapy
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