P.162 Clinical outcome study of dysferlinopathy: Performance of upper limb entry item to predict forced vital capacity in dysferlinopathy (LGMDR2) by James, M., Dressman, H. Gordish, Hilsden, H., Rufibach, L., Human, A., Duong, T., Maron, E., DeWolf, B., Rose, K., Siener, C., Thiele, S., Práxedes, N. Sánchez-Aguilera, Canal, A., Holsten, S., Sakamoto, C., Pedrosa-Hernández, I., Bello, L., Alfano, L., Lowes, L. Pax, Straub, V., Mayhew, A.

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North Star Assessment for dysferlinopathy: Longitudinal performance in the clinical outcome study of dysferlinopathy by James, M., Mayhew, A., Eagle, M., Muni Lofra, R., Maron, E., Gee, R., Harman, M., Duong, T., Vandevelde, B., Siener, C., Thiele, S., Mendez, J., Canal, A., Sakamoto, C., Holsten, S., Pedrosa-Hernández, I., Semplicini, C., Lowes, L., Bushby, K., Straub, V.

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P.161 - North Star Assessment for dysferlinopathy: Longitudinal performance in the clinical outcome study of dysferlinopathy by James, M., Mayhew, A., Eagle, M., Muni Lofra, R., Maron, E., Gee, R., Harman, M., Duong, T., Vandevelde, B., Siener, C., Thiele, S., Mendez, J., Canal, A., Sakamoto, C., Holsten, S., Pedrosa-Hernández, I., Semplicini, C., Lowes, L., Bushby, K., Straub, V.

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P.164 Clinical outcome study of dysferlinopathy 2: Characterising involvement of the intrinsic muscles of the hand in LGMDR2 by James, M., Mayhew, A., Gordish-Dressman, H., Rufibach, L., Wong, K., Roper, W., Holsten, S., Lowes, L., Duong, T., Yochai, C., Pardo, A. Zabala, Ogasawara, Y., Rudolph, K., Alarcon, S., Weber, J., Morillo, E. Montiel, Pedrosa-Hernandez, I., Birnbaum, S., Rojas, J. Rojas, Day, J., Straub, V.

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Performance of upper limb entry item to predict forced vital capacity in dysferlin-deficient limb girdle muscular dystrophy by Borland, Holly, Moore, Ursula, Dressman, Heather Gordish, Human, Anri, Mayhew, Anna G., Hilsden, Heather, Rufibach, Laura E., Duong, Tina, Maron, Elke, DeWolf, Brittney, Rose, Kristy, Siener, Catherine, Thiele, Simone, Práxedes, Nieves Sanchez-Aguilera, Canal, Aurélie, Holsten, Scott, Sakamoto, Chikako, Pedrosa-Hernández, Irene, Bello, Luca, Alfano, Lindsay N, Lowes, Linda Pax, James, Meredith K., Straub, Volker

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Correlation Between Respiratory Accessory Muscles and Diaphragm Pillars MRI and Pulmonary Function Test in Late-Onset Pompe Disease Patients by Reyes-Leiva, David, Alonso-Pérez, Jorge, Mayos, Mercedes, Nuñez-Peralta, Claudia, Llauger, Jaume, Belmonte, Izaskun, Pedrosa-Hernández, Irene, Segovia, Sonia, Díaz-Manera, Jordi

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Validity of Self-rating Screening Scales for the Diagnosis of Depression and Anxiety in Adult Patients With Bronchiectasis by Colomo, Natalia, Olveira, Casilda, Hernández-Pedrosa, Javier, Bergero, Trinidad, Fábrega-Ruz, Julia, Porras, Nuria, Girón, María Victoria, de Rota, Luis Fernández, Olveira, Gabriel

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Assessing Dysferlinopathy Patients Over Three Years With a New Motor Scale by Jacobs, Marni B., James, Meredoith K., Lowes, Linda P., Alfano, Lindsay N., Eagle, Michelle, Muni Lofra, Robert, Moore, Ursula, Feng, Jia, Rufibach, Laura E., Rose, Kristy, Duong, Tina, Bello, Luca, Pedrosa‐Hernández, Irene, Holsten, Scott, Sakamoto, Chikako, Canal, Aurélie, Sanchez‐Aguilera Práxedes, Nieves, Thiele, Simone, Siener, Catherine, Vandevelde, Bruno, DeWolf, Brittney, Maron, Elke, Guglieri, Michela, Hogrel, Jean‐Yves, Blamire, Andrew M., Carlier, Pierre G., Spuler, Simone, Day, John W., Jones, Kristi J., Bharucha‐Goebel, Diana X., Salort‐Campana, Emmanuelle, Pestronk, Alan, Walter, Maggie C., Paradas, Carmen, Stojkovic, Tanya, Mori‐Yoshimura, Madoka, Bravver, Elena, Díaz‐Manera, Jordi, Pegoraro, Elena, Mendell, Jerry R., Mayhew, Anna G., Straub, Volker

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Study of the effect of anti-rhGAA antibodies at low and intermediate titers in late onset Pompe patients treated with ERT by Fernández-Simón, Esther, Carrasco-Rozas, Ana, Gallardo, Eduard, González-Quereda, Lidia, Alonso-Pérez, Jorge, Belmonte, Izaskun, Pedrosa-Hernández, Irene, Montiel, Elena, Segovia, Sonia, Suárez-Calvet, Xavier, Llauger, Jaume, Mayos, Mercedes, Illa, Isabel, Barba-Romero, Miguel Angel, Barcena, Joseba, Paradas, Carmen, Carzorla, María Rosario, Creus, Carlota, Coll-Cantí, Jaume, Díaz, Manuel, Domínguez, Cristina, Fernández-Torrón, Roberto, García-Antelo, Maria José, Grau, Josep Maria, López de Munáin, Adolfo, Martínez-García, Francisco Antonio, Morgado, Yolanda, Moreno, Antonio, Morís, Germán, Muñoz-Blanco, Miguel Angel, Nascimento, Andres, Parajuá-Pozo, José Luis, Querol, Luis, Rojas, Ricard, Robledo-Strauss, Arturo, Rojas-Marcos, Íñigo, Salazar, Jose António, Usón, Mercedes, Díaz-Manera, Jordi

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Identification of serum microRNAs as potential biomarkers in Pompe disease by Carrasco‐Rozas, Ana, Fernández‐Simón, Esther, Lleixà, Maria Cinta, Belmonte, Izaskun, Pedrosa-Hernandez, Irene, Montiel-Morillo, Elena, Nuñez‐Peralta, Claudia, Llauger Rossello, Jaume, Segovia, Sonia, De Luna, Noemí, Suarez‐Calvet, Xavier, Illa, Isabel, Díaz‐Manera, Jordi, Gallardo, Eduard, Barba‐Romero, Miguel Angel, Barcena, Joseba, Carzorla, María Rosario, Creus, Carlota, Coll‐Cantí, Jaume, Díaz, Manuel, Domínguez, Cristina, Torrón, Roberto Fernández, García Antelo, María José, Grau, Josep María, Gómez Caravaca, María Teresa, León Hernández, Juan Carlos, López de Munáin, Adolfo, Martínez‐García, Francisco Antonio, Morgado, Yolanda, Moreno, Antonio, Muñoz‐Blanco, Miguel Angel, Nascimento, Andres, Paradas, Carmen, Parajuá Pozo, José Luis, Querol, Luis, Robledo‐Strauss, Arturo, García, Ricard Rojas, Rojas‐Marcos, Íñigo, Salazar, Jose Antonio, Usón, Mercedes

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Validity of Self-rating Screening Scales for the Diagnosis of Depression and Anxiety in Adult Patients With Bronchiectasis by Colomo, Natalia, Olveira, Casilda, Hernández-Pedrosa, Javier, Bergero, Trinidad, Fábrega-Ruz, Julia, Porras, Nuria, Girón, María Victoria, de Rota, Luis Fernández, Olveira, Gabriel

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Needs, Perceived Support, and Hospital Readmissions in Patients with Severe Mental Illness by Guzman-Parra, Jose, Moreno-Küstner, Berta, Rivas, Fabio, Alba-Vallejo, Mercedes, Hernandez-Pedrosa, Javier, Mayoral-Cleries, Fermin

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