128P Treatment with gene therapy in patients with spinal muscular atrophy. current experience in CuidAME registry by Exposito Escudero, J., Costa Comellas, L., García Romero, M., Toledo Bravo De Laguna, L., Gomez Martin, H., Calvo Medina, R., Navarro Abia, V., Ñungo Garzón, C., Martinez Gonzalez, M., Martínez Salcedo, E., Grimalt Calatayud, M., Martínez González, M., Álvarez Molinero, M., Fernández García, M., Puig Ram, C., Garcia Uzquiano, R., Hervás, D., Nascimento Osorio, A.

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P78 CuidAME: Three-year Spanish longitudinal project to collect data on patients with spinal muscular atrophy by Nascimento, A., Exposito, J., Segovia-Simón, S., Puig-Ram, C., Fernández - Cuesta, J., Garcia, M Fernandez, Lungo, C., Pitarch-Castellano, I., Pascual, S., Marco, C., Gonzalez, L., Povedano, M., Ballester, A., Martinez, E., Pareja, A., López-Lobato, M., Alvarez, M., Grimalt, M., Costa, J.

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