A Phase 1/2 Trial of Investigational Spk-8011 in Hemophilia a Demonstrates Durable Expression and Prevention of Bleeds by High, Katherine A., George, Lindsey A., Eyster, M. Elaine, Sullivan, Spencer K., Ragni, Margaret V., Croteau, Stacy E., Samelson-Jones, Ben J., Evans, Matthew, Joseney-Antoine, Marcelyne, Macdougall, Amy, Kadosh, Judith, Runoski, Alexa R., Campbell-Baird, Cynthia, Douglas, Kayla, Tompkins, Summer, Hait, Howard, Couto, Linda B., Bassiri, Ashlyn Eaton, Valentino, Leonard A., Carr, Marcus E., Hui, Daniel J, Wachtel, Katie, Takefman, Daniel, Mingozzi, Federico, Anguela, Xavier M., Reape, Kathleen B

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Spk-8011: Preliminary Results from a Phase 1/2 Dose Escalation Trial of an Investigational AAV-Mediated Gene Therapy for Hemophilia a by George, Lindsey A., Ragni, Margaret V., Samelson-Jones, Ben J., Cuker, Adam, Runoski, Alexa R., Cole, Grace, Wright, Fraser, Chen, Yifeng, Hui, Daniel J, Wachtel, Katie, Takefman, Daniel, Couto, Linda B., Reape, Kathleen Z., Carr, Marcus E., Anguela, Xavier M., High, Katherine A.

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Spk-9001: Adeno-Associated Virus Mediated Gene Transfer for Hemophilia B - 1 Year Follow up and Impact of Baseline Characteristics on Transgene-Derived Factor IX Activity and Persi... by George, Lindsey A., Sullivan, Spencer K., Giermasz, Adam, Samelson-Jones, Ben J., Ducore, Jonathan M., Teitel, Jerome M., Cuker, Adam, Von Mackensen, Sylvia, Majumdar, Suvankar, McGuinn, Catherine E., Runoski, Alexa R., Wright, Fraser, Dasen, Sue, Barber, Kimberly, Chen, Yifeng, Hui, Daniel J., Patel, Ruchi, Liu, Yun, Wachtel, Katie, Takefman, Dan, Couto, Linda B., Reape, Kathleen Z., Carr, Marcus E., Anguela, Xavier M., High, Katherine A.

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