Gene therapy for immune tolerance induction in hemophilia with inhibitors by Arruda, V. R., Samelson‐Jones, B. J.

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PL3‐AM23‐SN‐30 | Durable Elimination of Pre‐existing Donor‐Specific Alloantibodies Using Chimeric Antigen Receptors T Cells Targeting B cells and Long‐Lived Plasma Cells... by Bhoj, V., Zhang, Z., Markmann, C., Agarwal, D., Fraietta, J., Samelson‐Jones, B., Milone, M., Monos, D., Garfall, A., Naji, A.

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Enhanced procoagulant activity of select hemophilia B causing factor IX variants with emicizumab by Lee, Kyumin, Chau, Julia Q., Suber, Yani B., Sternberg, Anna R., Pishko, Allyson M., George, Lindsey A., Bhoj, Vijay G., Doshi, Bhavya S., Samelson-Jones, Benjamin J.

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PB0188 Improved Quality of Life in People with Hemophilia A Following Gene Therapy with Dirloctocogene Samoparvovec (SPK-8011) by Ragni, M., Evans, M., Croteau, S., Tran, H., Samelson-Jones, B., Teitel, J., Rasko, J., Sullivan, S., Moormeier, J., Haley, K., Jaworski, K., MacDougall, A., Long, A., Jaeger, S., Chang, T., Levy, G.

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OC 20.3 Improved Joint Health After Gene Therapy with Dirloctocogene Samoparvovec (SPK-8011) in People with Hemophilia A by Samelson-Jones, B., Ragni, M., Rasko, J., Haley, K., Croteau, S., Teitel, J., Tran, H., Cygan, P., Sullivan, S., Moormeier, J., Jaeger, S., Long, A., Levy, G., MacDougall, A., Jaworski, K., Chang, T.

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A Phase 1/2 Trial of Investigational Spk-8011 in Hemophilia a Demonstrates Durable Expression and Prevention of Bleeds by High, Katherine A., George, Lindsey A., Eyster, M. Elaine, Sullivan, Spencer K., Ragni, Margaret V., Croteau, Stacy E., Samelson-Jones, Ben J., Evans, Matthew, Joseney-Antoine, Marcelyne, Macdougall, Amy, Kadosh, Judith, Runoski, Alexa R., Campbell-Baird, Cynthia, Douglas, Kayla, Tompkins, Summer, Hait, Howard, Couto, Linda B., Bassiri, Ashlyn Eaton, Valentino, Leonard A., Carr, Marcus E., Hui, Daniel J, Wachtel, Katie, Takefman, Daniel, Mingozzi, Federico, Anguela, Xavier M., Reape, Kathleen B

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Spk-8011: Preliminary Results from a Phase 1/2 Dose Escalation Trial of an Investigational AAV-Mediated Gene Therapy for Hemophilia a by George, Lindsey A., Ragni, Margaret V., Samelson-Jones, Ben J., Cuker, Adam, Runoski, Alexa R., Cole, Grace, Wright, Fraser, Chen, Yifeng, Hui, Daniel J, Wachtel, Katie, Takefman, Daniel, Couto, Linda B., Reape, Kathleen Z., Carr, Marcus E., Anguela, Xavier M., High, Katherine A.

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Spk-9001: Adeno-Associated Virus Mediated Gene Transfer for Hemophilia B - 1 Year Follow up and Impact of Baseline Characteristics on Transgene-Derived Factor IX Activity and Persi... by George, Lindsey A., Sullivan, Spencer K., Giermasz, Adam, Samelson-Jones, Ben J., Ducore, Jonathan M., Teitel, Jerome M., Cuker, Adam, Von Mackensen, Sylvia, Majumdar, Suvankar, McGuinn, Catherine E., Runoski, Alexa R., Wright, Fraser, Dasen, Sue, Barber, Kimberly, Chen, Yifeng, Hui, Daniel J., Patel, Ruchi, Liu, Yun, Wachtel, Katie, Takefman, Dan, Couto, Linda B., Reape, Kathleen Z., Carr, Marcus E., Anguela, Xavier M., High, Katherine A.

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