Search Results - Viecelli, Hiu-Man

  • Showing 1 - 12 results of 12
Refine Results
  1. 1
    Computationally designed liver-specific transcriptional modules and hyperactive factor IX improve hepatic gene therapy

    Computationally designed liver-specific transcriptional modules and hyperactive factor IX improve hepatic gene therapy by Nair, Nisha, Rincon, Melvin Y., Evens, Hanneke, Sarcar, Shilpita, Dastidar, Sumitava, Samara-Kuko, Emira, Ghandeharian, Omid, Man Viecelli, Hiu, Thöny, Beat, De Bleser, Pieter, VandenDriessche, Thierry, Chuah, Marinee K.

    Published in Blood
    Get full text
    Items that this one cites
    Items that cite this one
    Article
    Save to List
    Saved in:
  2. 2
    Functional characterization of the spf/ash splicing variation in OTC deficiency of mice and man

    Functional characterization of the spf/ash splicing variation in OTC deficiency of mice and man by Rivera-Barahona, Ana, Sánchez-Alcudia, Rocío, Viecelli, Hiu Man, Rüfenacht, Veronique, Pérez, Belén, Ugarte, Magdalena, Häberle, Johannes, Thöny, Beat, Desviat, Lourdes Ruiz

    Published in PloS one
    Get full text
    Items that this one cites
    Items that cite this one
    Article
    Save to List
    Saved in:
  3. 3
    Correction: Functional Characterization of the spf/ash Splicing Variation in OTC Deficiency of Mice and Man

    Correction: Functional Characterization of the spf/ash Splicing Variation in OTC Deficiency of Mice and Man by Rivera-Barahona, Ana, Sánchez-Alcudia, Rocío, Viecelli, Hiu Man, Rüfenacht, Veronique, Pérez, Belén, Ugarte, Magdalena, Häberle, Johannes, Thöny, Beat, Desviat, Lourdes Ruiz

    Published in PloS one
    Get full text
    Article
    Save to List
    Saved in:
  4. 4
    A Sensitive Assay System To Test Antisense Oligonucleotides for Splice Suppression Therapy in the Mouse Liver

    A Sensitive Assay System To Test Antisense Oligonucleotides for Splice Suppression Therapy in the Mouse Liver by Gallego-Villar, Lorena, Viecelli, Hiu Man, Pérez, Belén, Harding, Cary O, Ugarte, Magdalena, Thöny, Beat, Desviat, Lourdes R

    Get full text
    Items that this one cites
    Items that cite this one
    Article
    Save to List
    Saved in:
  5. 5
    169. Expression Studies of Ornithine Transcarbamylase in Liver Using Minicircle Vectors for Gene Therapy: Flag-Tagging of a Mitochondrial Enzyme and Stable Expression Under Control of an Endogenous Otc Promoter-Enhancer

    169. Expression Studies of Ornithine Transcarbamylase in Liver Using Minicircle Vectors for Gene Therapy: Flag-Tagging of a Mitochondrial Enzyme and Stable Expression Under Control... by Viecelli, Hiu Man, Deplazes, Sereina, Schlegel, Andrea, Cunningham, Sharon, Alexander, Ian, Häberle, Johannes, Thöny, Beat

    Published in Molecular therapy
    Get full text
    Article
    Save to List
    Saved in:
  6. 6
    355. Minicircles Show Improved Hepatic Expression of Their Transgene from a Natural Endogenous Promoter and Are Lost Upon Partial Hepatectomy Due to the Episomal Nature of the Vector

    355. Minicircles Show Improved Hepatic Expression of Their Transgene from a Natural Endogenous Promoter and Are Lost Upon Partial Hepatectomy Due to the Episomal Nature of the Vect... by Viecelli, Hiu-Man, Schlegel, Andrea, Scherer, Tanja, Allegri, Gabirella, Schleef, Martin, Harding, Cary O, Häberle, Johannes, Thöny, Beat

    Published in Molecular therapy
    Get full text
    Article
    Save to List
    Saved in:
  7. 7
    150. Liver Directed Gene Therapy Using Non-Viral Minicircle-DNA Vector for Ornithine Transcarbamylase Deficiency (OTCD)

    150. Liver Directed Gene Therapy Using Non-Viral Minicircle-DNA Vector for Ornithine Transcarbamylase Deficiency (OTCD) by Man Viecelli, Hiu, Schlegel, Andrea, Deplazes, Sereina, Cunningham, Sharon, Alexander, Ian, Häberle, Johannes, Thöny, Beat

    Published in Molecular therapy
    Get full text
    Article
    Save to List
    Saved in:
  8. 8
    146. Optimizing Safety and Long-Term Efficacy of Liver Gene Therapy With Non-Integrating Naked-DNA Minicircle Vectors Expressing Their Transgene from a Natural Promoter

    146. Optimizing Safety and Long-Term Efficacy of Liver Gene Therapy With Non-Integrating Naked-DNA Minicircle Vectors Expressing Their Transgene from a Natural Promoter by Man Viecelli, Hiu, Schlegel, Andrea, Scherer, Tanja, Schleef, Martin, Harding, Cary O., Thöny, Beat

    Published in Molecular therapy
    Get full text
    Article
    Save to List
    Saved in:
  9. 9
    358. Non-Viral/Minicircle Vector Transduction of Hepatocytes in Small Pigs By Hydrodynamic Intraportal Injection

    358. Non-Viral/Minicircle Vector Transduction of Hepatocytes in Small Pigs By Hydrodynamic Intraportal Injection by Man Viecelli, Hiu, Stoller, Fabienne, Schlegel, Andrea, Rüfenacht, Veronique, Cesarovic, Nikola, Viecelli, Claudio, Deplazes, Sereina, Sidler, Xaver, Kron, Philipp, Dutkowski, Philipp, Graf, Rolf, Thöny, Beat, Häberle, Johannes

    Published in Molecular therapy
    Get full text
    Article
    Save to List
    Saved in:
  10. 10
    Functional Characterization of the spf/ash Splicing Variation in OTC Deficiency of Mice and Man: e0122966

    Functional Characterization of the spf/ash Splicing Variation in OTC Deficiency of Mice and Man: e0122966 by Rivera-Barahona, Ana, Sanchez-Alcudia, Rocio, Viecelli, Hiu Man, Ruefenacht, Veronique, Perez, Belen, Ugarte, Magdalena, Haeberle, Johannes, Thony, Beat, Desviat, Lourdes Ruiz

    Published in PloS one
    Get full text
    Article
    Save to List
    Saved in:
  11. 11
    Functional Characterization of the spf/ash Splicing Variation in OTC Deficiency of Mice and Man

    Functional Characterization of the spf/ash Splicing Variation in OTC Deficiency of Mice and Man by Rivera-Barahona, Ana, Sánchez-Alcudia, Rocío, Viecelli, Hiu Man, Rüfenacht, Veronique, Pérez, Belén, Ugarte, Magdalena, Häberle, Johannes, Thöny, Beat, Desviat, Lourdes Ruiz

    Published in PLoS ONE
    Get full text
    Report
    Save to List
    Saved in:
  12. 12
    Functional Characterization of the spf/ash Splicing Variation in OTC Deficiency of Mice and Man

    Functional Characterization of the spf/ash Splicing Variation in OTC Deficiency of Mice and Man by Rivera-Barahona, Ana, Sánchez-Alcudia, Rocío, Viecelli, Hiu Man, Rüfenacht, Veronique, Pérez, Belén, Ugarte, Magdalena, Häberle, Johannes, Thöny, Beat, Desviat, Lourdes Ruiz

    Published in PLoS ONE
    Get full text
    Report
    Save to List
    Saved in:

Search Tools: