Guidelines for diagnosis and treatment of Hunter Syndrome for clinicians in Latin America by Giugliani, Roberto, Villarreal, Martha Luz Solano, Valdez, C Araceli Arellano, Hawilou, Antonieta Mahfoud, Guelbert, Norberto, Garzón, Luz Norela Correa, Martins, Ana Maria, Acosta, Angelina, Cabello, Juan Francisco, Lemes, Aída, Santos, Mara Lucia Schmitz Ferreira, Amartino, Hernán

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A phase II/III intrathecal enzyme replacement therapy clinical trial for MPS II patients with cognitive impairment by Muenzer, Joseph, Burton, Barbara K., Harmatz, Paul, Villarreal, Martha Luz Solano, Amartino, Hernán M., Ruiz-Garcia, Matilde, Gutiérrez-Solana, Luis González, Sciarappa, Kenneth, Alexanderian, David, Jones, Simon A.

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Natural history data for young subjects with Sanfilippo syndrome type B (MPS IIIB) by Okur, Ilyas, Cleary, Maureen, de Castro Lopez, Maria Jose, Harmatz, Paul, Lee, Joy, Lin, Shaun-Pei, Couce, Maria Luz, Muschol, Nicole, Peters, Heidi, Villarreal, Martha Solano, Shaywitz, Adam, Cahan, Heather, Grover, Anita, Maricich, Stephen M., Melton, Andrew, Smith, Lynn, Ezgu, Fatih

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ICV-administered tralesinidase alfa (BMN 250 NAGLU-IGF2) is well-tolerated and reduces heparan sulfate accumulation in the CNS of subjects with Sanfilippo syndrome type B (MPS IIIB... by Cleary, Maureen, Muschol, Nicole, Couce, Maria Luz, Harmatz, Paul, Lee, Joy, Lin, Shuan-Pei, Okur, Ilyas, Ezgu, Fatih, Peters, Heidi, Villarreal, Martha Solano, Shaywitz, Adam J., Cahan, Heather, Grover, Anita, Melton, Andrew, Smith, Lynn, Maricich, Stephen M., de Castro Lopez, Maria J.

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Natural history data for young subjects with Sanfilippo syndrome type B (MPS IIIB) by Villarreal, Martha Solano, Okur, Ilyas, Cleary, Maureen, de Castro Lopez, Maria Jose, Harmatz, Paul, Lee, Joy, Lin, Shuan-Pei, Couce, Maria Luz, Muschol, Nicole, Peters, Heidi, Shaywitz, Adam J., Cahan, Heather, Grover, Anita, Melton, Andrew, Smith, Lynn, Maricich, Stephen M., Ezgu, Fatih

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