ETV:SGSH, a brain-penetrant enzyme transport vehicle for SGSH, corrects heparan sulfate accumulation, lysosomal lipid storage and inflammation in MPS IIIA mouse brain by Masoud, Shababa T., Jafarnejad, Mohammad, Nguyen, Hoang, Tsogtbaatar, Buyankhishig, Rajendra, Yashas, Seay, Alexander, Thomsen, Elliot R., Yamanokuchi, Kensuke, Arguello, Annie, Fang, Meng, Mahon, Cathal S., Sanchez, Pascal, Diaz, Dolo, Bakardjiev, Anna, Henne, Kirk

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