O.6Pre-clinical development of SPK-3006, an investigational liver-directed AAV gene therapy for the treatment of Pompe disease

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Bibliographic Details
Published in:Neuromuscular disorders : NMD 2019-10, Vol.29, p.S39-S39
Main Authors: Armour, S., Nordin, J., Costa Verdera, H., Cohen, D., Sellier, P., Crosariol, M., Collaud, F., Riling, C., Quinn, W., Hanby, H., Cagin, U., Puzzo, F., Haurigot, V., Ronzitti, G., Colella, P., Anguela, X., Mingozzi, F.
Format: Article
Language:English
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ISSN:0960-8966
1873-2364
DOI:10.1016/j.nmd.2019.06.024