ZFN-mediated in vivo genome editing of hepatocytes results in phenotypic correction in murine MPS I and MPS II models

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Bibliographic Details
Published in:Molecular genetics and metabolism 2018-02, Vol.123 (2), p.S146-S147
Main Authors: Wechsler, Thomas, DeKelver, Russell, Laoharawee, Kanut, Ou, Li, Tom, Susan, Radecke, Robert, Sproul, Scott, Koniar, Brenda L., Podetz-Perdersen, Kelly, Cooksley, Renee D., Meyer, Kathleen, McIvor, Scott R., Chester, Whitley B., Holmes, Michael C.
Format: Article
Language:English
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ISSN:1096-7192
1096-7206
DOI:10.1016/j.ymgme.2017.12.405