Systemic high-level IDUA enzyme activity with correction of neurologic deficit in mucopolysaccharidosis type I mice by lentiviral transduction of hematopoietic stem cells

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Bibliographic Details
Published in:Molecular genetics and metabolism 2020-02, Vol.129 (2), p.S30-S31
Main Authors: Belur, Lalitha, McKenzie, Jessica, Podetz-Pedersen, Kelly, Karlen, Andrea, de Souza, Patricia Coutinho, LaBarre, Shelby, Smith, Miles, Huber, Avery, Detellis, Jennifer, Gagnidze, Khatuna, Parsons, Geoff, Tsai, Hsing-Chen, McIvor, R. Scott, Bonner, Melissa
Format: Article
Language:English
Online Access:Get full text
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ISSN:1096-7192
DOI:10.1016/j.ymgme.2019.11.052