Baseline patient characteristics of followME, a new, patient-centric, prospective, observational Fabry disease registry that evaluates migalastat, ERT, and a natural history cohort

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Bibliographic Details
Published in:Molecular genetics and metabolism 2020-02, Vol.129 (2), p.S150-S150
Main Authors: Sunder-Plassmann, Gere, Bichet, Daniel G., Davidonis, Martynas, Germain, Dominique P., Giugliani, Roberto, Hopkin, Robert J., Jovanovic, Ana, Linhart, Ales, Nicholls, Kathleen, Nordbeck, Peter, Feldt-Rasmussen, Ulla, Rutecki, Jasmine, Giuliano, Joe, Skuban, Nina, Krusinska, Eva, Politei, Juan
Format: Article
Language:English
Online Access:Get full text
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ISSN:1096-7192
1096-7206
DOI:10.1016/j.ymgme.2019.11.397