AT845 gene replacement therapy for late onset Pompe disease: Overview of clinical data from FORTIS, a phase 1/2 open-label clinical study

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Bibliographic Details
Published in:Molecular genetics and metabolism 2022-02, Vol.135 (2), p.S85-S86
Main Authors: Mozaffar, Tahseen, Day, John W., Longo, Nicola, Manera, Jordi Diaz, Straub, Volker, Maruoka, Miko, Han, Cong, Foo, Cheryl Wong Po, Smith, Angela R., Bachtell, Nathan
Format: Article
Language:English
Online Access:Get full text
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ISSN:1096-7192
1096-7206
DOI:10.1016/j.ymgme.2021.11.221