A structurally targeted allosteric regulator of GCase restores enzyme activity, reduces microgliosis, and improves fine locomotor skills in the CBE model of neuronopathic Gaucher disease

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Bibliographic Details
Published in:Molecular genetics and metabolism 2023-02, Vol.138 (2), p.107133, Article 107133
Main Authors: Guzman, Beatriz, Pérez, Natalia, Garcia-Collazo, Ana Maria, Cubero, Elena, Barril, Xavier, Bellotto, Manolo, Taylor, Joanne
Format: Article
Language:English
Online Access:Get full text
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ISSN:1096-7192
1096-7206
DOI:10.1016/j.ymgme.2022.107133