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STAAR, a phase I/II study of isaralgagene civaparvovec (ST-920) gene therapy in adults with Fabry disease: Dose escalation phase results

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Bibliographic Details
Published in:Molecular genetics and metabolism 2023-02, Vol.138 (2), p.107152, Article 107152
Main Authors: Hopkin, Robert J., Ganesh, Jaya, Deegan, Patrick, Goker-Alpan, Ozlem, Bernat, John, Wilcox, William R., Pahl, Madeleine V., Whitley, Chester B., Hughes, Derralynn, Nicholls, Kathleen, Cao, Liching, Chen, Michael, Shiue, Lisa H., Bowden, Emma, Jaggumantri, Sravan, Passalacqua, Cristobal, Souberbielle, Bernard, Cockroft, Bettina M.
Format: Article
Language:English
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ISSN:1096-7192
1096-7206
DOI:10.1016/j.ymgme.2022.107152