Long-term outcomes of MPS IVA patients treated with elosulfase alfa: Findings from the Morquio A Registry Study (MARS) after 10 years

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Bibliographic Details
Published in:Molecular genetics and metabolism 2025-02, Vol.144 (2), p.108859, Article 108859
Main Authors: Mitchell, John J., Burton, Barbara K., Campeau, Philippe M., Ellaway, Carolyn, Guffon, Nathalie, Hughes, Derralynn, Hunt, Abigail, Lail, Alice, Lin, Hsiang-Yu, Lin, Shuan-Pei, Magner, Martin, Reddy, Sheila, Reisewitz, Pascal, Stepien, Karolina M.
Format: Article
Language:English
Online Access:Get full text
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ISSN:1096-7192
DOI:10.1016/j.ymgme.2024.108859