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Hematopoietic and Immunological Assessment in Fanconi Anemia after Ex Vivo Lentiviral FANCA Gene Therapy with RP-L102

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Bibliographic Details
Published in:Blood 2022-11, Vol.140 (Supplement 1), p.7772-7773
Main Authors: Nofal, Rofida, Chan, Yan Yi, Sen, Sushmita, Juarez Figueroa, Ulises, Willner, Hana, Felber, Matthias, Krampf, Mark, Thongthip, Supawat, Choi, Grace, Nicoletti, Eileen, Schwartz, Jonathan D., Weinberg, Kenneth I., Rodriguez, Alfredo, Agarwal, Rajni, Roncarolo, Maria Grazia, Czechowicz, Agnieszka
Format: Article
Language:English
Online Access:Get full text
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ISSN:0006-4971
1528-0020
DOI:10.1182/blood-2022-157840