Safety and improved efficacy signals following gene therapy in childhood blindness caused by GUCY2D mutations

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Bibliographic Details
Published in:iScience 2024-11, Vol.27 (11), p.111048, Article 111048
Main Authors: Jacobson, Samuel G., Cideciyan, Artur V., Ho, Allen C., Peshenko, Igor V., Garafalo, Alexandra V., Roman, Alejandro J., Sumaroka, Alexander, Wu, Vivian, Krishnan, Arun K., Sheplock, Rebecca, Cheang, Bee-Lin, Davidson, Vanessa, O’Riordan, Catherine R., Boye, Sanford L., Dizhoor, Alexander M., Boye, Shannon E.
Format: Article
Language:English
Online Access:Get full text
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ISSN:2589-0042
2589-0042
DOI:10.1016/j.isci.2024.111048