P314: Long-term safety and sustained functional benefit in patients with DMD 4 years post-treatment with delandistrogene moxeparvovec: A phase 1/2a study

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Bibliographic Details
Published in:Genetics in Medicine Open 2023, Vol.1 (1), p.100342, Article 100342
Main Authors: O’Rourke, Erin, Mendell, Jerry R., Sahenk, Zarife, Lehman, Kelly J., Lowes, Linda P., Reash, Natalie F., Iammarino, Megan, Alfano, Lindsay, Lewis, Sarah, Church, Kathleen, Shell, Richard, Potter, Rachael A., Griffin, Danielle, Hogan, Mark J., Wang, Shufang, Mason, Stefanie, Darton, Eddie, Rodino-Klapac, Louise
Format: Article
Language:English
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ISSN:2949-7744
2949-7744
DOI:10.1016/j.gimo.2023.100342