Effect of Oral Eliglustat vs Placebo on Spleen Volume in Patients with Splenomegaly and Gaucher Disease Type 1: The ENGAGE Randomized Clinical Trial

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Bibliographic Details
Published in:JAMA : the journal of the American Medical Association 2015-02, Vol.313 (7), p.695-706
Main Authors: Mistry, Pramod K., Lukina, Elena, Turkia, Hadhami Ben, Amato, Dominick, Baris, Hagit, Dasouki, Majed, Ghosn, Marwan, Mehta, Atul, Packman, Seymour, Pastores, Gregory, Petakov, Milan, Assouline, Sarit, Balwani, Manisha, Danda, Sumita, Hadjiev, Evgueniy, Ortega, Andres, Shankar, Suma, Solano, Maria Helena, Ross, Leorah, Angell, Jennifer, Peterschmitt, M. Judith
Format: Article
Language:English
Online Access:Get full text
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ISSN:0098-7484
1538-3598
DOI:10.1001/jama.2015.459